6 studies found for: "Barth syndrome" OR "3 methylglutaconic aciduria, type II" OR "3-methylglutaconic aciduria type 2"
Exercise Training in Barth Syndrome
Heart and Muscle Metabolism in Barth Syndrome
Resistance Exercise in Barth Syndrome
A Trial to Evaluate Safety, Tolerability and Efficacy of Elamipretide in Subjects With Barth Syndrome
Compassionate Use of Triheptanoin (C7) for Inherited Disorders of Energy Metabolism
North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
† Study has passed its completion date and status has not been verified in more than two years.