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4 studies found for:    "Aromatic amino acid decarboxylase deficiency"
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Study Details
Participant Details
Identifiers
Dates
Rank Status Study
1 Completed Newborn Screening for Aromatic L-amino Acid Decarboxylase Deficiency
Condition: Aromatic L-amino Acid Decarboxylase Deficiency
Intervention:
2 Recruiting A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients
Condition: AADC Deficiency
Intervention: Drug: AAV2-hAADC
3 Recruiting A Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC - An Expansion
Condition: Aromatic Amino Acid Decarboxylase Deficiency
Intervention: Drug: AAV2-hAADC
4 Completed A Phase I/II Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC
Condition: Aromatic L-amino Acid Decarboxylase (AADC) Deficiency
Intervention: Drug: gene therapy

Study has passed its completion date and status has not been verified in more than two years.