4 studies found for: "Aromatic amino acid decarboxylase deficiency"
Newborn Screening for Aromatic L-amino Acid Decarboxylase Deficiency
A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients
A Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC - An Expansion
|4||Enrolling by invitation||
A Phase I/II Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC
† Indicates status has not been verified in more than two years