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639 studies found for:    "Anemia, Hemolytic, Congenital"
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Rank Status Study
1 Recruiting Improving the Results of Bone Marrow Transplantation for Patients With Severe Congenital Anemias
Conditions: Congenital Hemolytic Anemia;   Diamond-Blackfan Anemia
Interventions: Procedure: Radiotherapy;   Drug: Alemtuzumab (Campath );   Drug: Sirolimus (Rapamune )
2 Recruiting Fat and Sugar Metabolism During Exercise in Patients With Metabolic Myopathy
Conditions: Metabolism, Inborn Errors;   Lipid Metabolism, Inborn Errors;   Carbohydrate Metabolism, Inborn Errors;   Long-Chain 3-Hydroxyacyl-CoA Dehydrogenase Deficiency;   Glycogenin-1 Deficiency (Glycogen Storage Disease Type XV);   Carnitine Palmitoyl Transferase 2 Deficiency;   VLCAD Deficiency;   Medium-chain Acyl-CoA Dehydrogenase Deficiency;   Multiple Acyl-CoA Dehydrogenase Deficiency;   Carnitine Transporter Deficiency;   Neutral Lipid Storage Disease;   Glycogen Storage Disease Type II;   Glycogen Storage Disease Type III;   Glycogen Storage Disease Type IV;   Glycogen Storage Disease Type V;   Muscle Phosphofructokinase Deficiency;   Phosphoglucomutase 1 Deficiency;   Phosphoglycerate Mutase Deficiency;   Phosphoglycerate Kinase Deficiency;   Phosphorylase Kinase Deficiency;   Beta Enolase Deficiency;   Lactate Dehydrogenase Deficiency;   Glycogen Synthase Deficiency
Intervention: Other: Sugar
3 Recruiting A Study of AG-348 in Adult Patients With Pyruvate Kinase Deficiency
Condition: Pyruvate Kinase Deficiency
Intervention: Drug: AG-348
4 Recruiting Pyruvate Kinase Deficiency Natural History Study
Conditions: Pyruvate Kinase Deficiency;   Congenital Non-Spherocytic Hemolytic Anemia
5 Recruiting Evaluation of the AMICUS RBCx System in Sickle Cell Patients
Condition: Sickle Cell Anemia
Intervention: Device: Amicus Red Cell Exchange in SCD patients
6 Terminated The Dallas Hereditary Spherocytosis Cohort Study
Condition: Hereditary Spherocytosis
7 Not yet recruiting Effects of N-acetyl Cystein (NAC) Supplementation in G6PD Deficient Individuals After Acute Exercise
Condition: G6PD Deficiency
Interventions: Drug: N-acetyl cystein;   Other: Placebo
8 Not yet recruiting Effects of Alpha Lipoic Acid Supplementation in G6PD Deficient Individuals After Acute Exercise
Condition: G6PD Deficiency
Interventions: Dietary Supplement: Alpha-lipoic acid;   Other: Placebo
9 Recruiting Glucose Metabolism in Sickle Cell Disease
Conditions: Sickle Cell Disease;   Diabetes Mellitus
10 Completed Sickle Cell Anemia and Cerebral Microcirculation : Multimodal Exploration
Condition: Sickle Cell Disease
Intervention: Procedure: Physical exams and blood analyzes
11 Recruiting A Study Evaluating the Efficacy and Safety of the LentiGlobin® BB305 Drug Product in Subjects With Transfusion-Dependent β-Thalassemia
Condition: Beta-Thalassemia
Intervention: Genetic: LentiGlobin BB305 Drug Product
12 Recruiting The Prevalence and Severity of HCV Infection in Thalassemia Major and Thalassemia Intermedia in Siriraj Hospital
Conditions: Hepatitis C;   Fibrosis;   Thalassemia
Intervention: Other: Transient elastography
13 Recruiting Dense Red Blood Cells in Sickle Cell Children
Condition: Sickle Cell Disease
14 Completed Study of Hydroxyurea to Treat Sickle Cell Disease
Condition: Sickle Cell Disease
15 Recruiting Abatacept for GVHD Prophylaxis After Hematopoietic Stem Cell Transplantation for Pediatric Sickle Cell Disease
Conditions: Sickle Cell Disease;   Graft Versus Host Disease
Interventions: Drug: Diphenhydramine;   Drug: Acetaminophen;   Drug: Methylprednisolone;   Drug: Meperidine;   Drug: Alemtuzumab;   Drug: Thymoglobulin;   Drug: Fludarabine;   Drug: Melphalan;   Drug: Thiotepa;   Drug: Cyclosporine;   Drug: Tacrolimus;   Drug: Methotrexate;   Drug: Abatacept;   Procedure: Marrow infusion
16 Not yet recruiting Topical Sodium Nitrite in Sickle Cell Disease and Leg Ulcers
Condition: Sickle Cell Disease
Interventions: Drug: Topical Sodium Nitrite;   Other: Placebo
17 Recruiting Feasibility and Efficacy of a Home-based, Computerized Cognitive Training Program in Pediatric Sickle Cell Disease
Condition: Anemia, Sickle Cell
Intervention: Behavioral: Cogmed RM
18 Recruiting Improving Self-Management in Adolescents With Sickle Cell Disease
Condition: Sickle Cell Disease
Intervention: Behavioral: SCThrive Intervention for Adolescents with SCD
19 Recruiting Study to Evaluate the Effect of GBT440 in Adolescents With Sickle Cell Disease
Condition: Sickle Cell Disease
Intervention: Drug: GBT440
20 Not yet recruiting Mobile-Directly Observed Therapy on Adherence to Hydroxyurea
Condition: Sickle Cell Anaemia
Interventions: Drug: Hydroxyurea;   Device: Mobile Directly Observed Therapy

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