Key Record Dates
ClinicalTrials.gov Identifier: | NCT04669535 |
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Brief Title: | A Dose-escalation and Safety & Efficacy Study of AXO-AAV-GM2 in Tay-Sachs or Sandhoff Disease |
First Submitted : | November 23, 2020 |
First Submitted that Met QC Criteria : | December 8, 2020 |
First Posted : | December 17, 2020 |
Last Update Submitted that Met QC Criteria : | January 26, 2021 |
Last Update Posted : | January 29, 2021 |