Key Record Dates
ClinicalTrials.gov Identifier: | NCT03837184 |
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Brief Title: | Single-Dose Gene Replacement Therapy Using for Patients With Spinal Muscular Atrophy Type 1 With One or Two SMN2 Copies |
First Submitted : | February 8, 2019 |
First Submitted that Met QC Criteria : | February 8, 2019 |
First Posted : | February 12, 2019 |
Last Update Submitted that Met QC Criteria : | March 26, 2021 |
Last Update Posted : | March 30, 2021 |