Registry to Monitor the Susceptibility to Aztreonam of Pseudomonas Aeruginosa Isolates From Cystic Fibrosis Patients (AIR-CF5)

This study is ongoing, but not recruiting participants.
Sponsor:
Collaborator:
Cystic Fibrosis Foundation
Information provided by (Responsible Party):
Gilead Sciences
ClinicalTrials.gov Identifier:
NCT01375036
First received: June 15, 2011
Last updated: December 13, 2012
Last verified: December 2011
  Purpose

This is a 5-year study that will enroll 500 subjects from the existing Cystic Fibrosis Foundation (CFF) patient registry. Eligible subjects will be patients who receive care at CFF-accredited centers nationwide. Each enrolled subject will provide samples for microbiological evaluation, obtained upon enrollment and then once per year thereafter for 5 years.


Condition
Cystic Fibrosis

Study Type: Observational
Study Design: Time Perspective: Prospective
Official Title: A Prospective, 5-year Registry Study to Monitor the Susceptibility to Aztreonam of Pseudomonas Aeruginosa (PA) Isolates From Patients With Cystic Fibrosis in the United States [AIR-CF5]

Resource links provided by NLM:


Further study details as provided by Gilead Sciences:

Primary Outcome Measures:
  • Changes in susceptibility among Pseudomonas aeruginosa (PA) isolates to aztreonam [ Time Frame: 5 years ] [ Designated as safety issue: No ]
    To determine whether there are any changes in susceptibility to aztreonam among Pseudomonas aeruginosa (PA) isolates from subjects with cystic fibrosis (CF) in the United States over the five year period after introduction of Cayston® (aztreonam for inhalation solution).


Secondary Outcome Measures:
  • Determine whether changes in clinical outcomes are associated with changes in susceptibility of PA isolates to aztreonam. [ Time Frame: 5 years ] [ Designated as safety issue: No ]
    The secondary objective is to determine whether any changes in susceptibility are associated with changes in clinical outcomes, including changes in lung function, number and duration of hospitalizations, and body mass index (BMI).


Biospecimen Retention:   Samples Without DNA

Pseudomonas aeruginosa isolates from sputum or throat swab specimens


Estimated Enrollment: 500
Study Start Date: August 2011
Estimated Study Completion Date: February 2017
Estimated Primary Completion Date: August 2016 (Final data collection date for primary outcome measure)
Detailed Description:

This is a prospective, longitudinal study that will enroll a subset of subjects from the existing Cystic Fibrosis Foundation (CFF) patient registry, which includes more than 25,500 patients who receive care at CFF-accredited centers nationwide. This will be a 5-year study embedded within the CFF registry that will include collection of lower respiratory tract samples from 500 subjects each year. These samples for microbiological evaluation will be obtained from each subject upon enrollment and then once per year thereafter.

  Eligibility

Ages Eligible for Study:   6 Years and older
Genders Eligible for Study:   Both
Accepts Healthy Volunteers:   No
Sampling Method:   Non-Probability Sample
Study Population

A representative cross-section of subjects with mild (FEV1 75% to

≤ 90% predicted), moderate (FEV1 40% to 74% predicted), or severe (FEV1 <40% predicted) lung disease and a history of ≥ 2 lower respiratory tract cultures positive for PA (at any time)will be enrolled. This will include approximately 100 subjects with pre-study exposure to Cayston (defined as having received at least one prior 28-day course of Cayston at any time before enrolling into the study). Enrollment will be monitored and potentially modified to ensure that adequate numbers of subjects in each disease severity category are included. At the Investigator's discretion, subjects enrolled in this study can be allowed to participate in clinical trials with other investigational therapies as appropriate.

Criteria

Inclusion Criteria:

Subjects must meet all of the following inclusion criteria to be eligible for participation in this study.

  • Current participant or willingness to participate in the CFF patient registry database
  • ≥ 6 years of age
  • Subject has CF as diagnosed by one of the following

    • Documented sweat chloride ≥ 60 mEq/L by quantitative pilocarpine iontophoresis test, or
    • Two well-characterized genetic mutations in the CFTR gene, or
    • Abnormal nasal potential difference (NPD) AND accompanying clinical characteristics consistent with CF. For subjects who lack documentation of either a positive sweat chloride test or an abnormal NPD, and who have only one well-characterized genetic mutation of the CFTR gene, the diagnosis of CF is determined by the Investigator.
  • FEV1 ≥ 25% predicted and ≤ 90% predicted.
  • ≥ 2 lower respiratory tract cultures positive for PA with results documented in the subject's medical history.
  • Subject must be able to provide written informed consent/assent prior to any study related procedure; parent/guardian must be able to give written informed consent as necessary prior to any study related procedure.

Exclusion Criteria:

Subjects who meet the following exclusion criterion are not to be enrolled in this study.

• Any serious active medical or psychiatric illness that, in the opinion of the Investigator, would interfere with subject assessment.

  Contacts and Locations
Please refer to this study by its ClinicalTrials.gov identifier: NCT01375036

  Show 31 Study Locations
Sponsors and Collaborators
Gilead Sciences
Cystic Fibrosis Foundation
Investigators
Study Director: Mark Bresnik, MD Gilead Sciences
  More Information

No publications provided

Responsible Party: Gilead Sciences
ClinicalTrials.gov Identifier: NCT01375036     History of Changes
Other Study ID Numbers: GX-US-205-0128
Study First Received: June 15, 2011
Last Updated: December 13, 2012
Health Authority: United States: Food and Drug Administration

Keywords provided by Gilead Sciences:
Cystic fibrosis
PA
Pseudomonas aeruginosa
CF
aztreonam

Additional relevant MeSH terms:
Cystic Fibrosis
Disease Susceptibility
Genetic Predisposition to Disease
Fibrosis
Pseudomonas Infections
Pancreatic Diseases
Digestive System Diseases
Lung Diseases
Respiratory Tract Diseases
Genetic Diseases, Inborn
Infant, Newborn, Diseases
Disease Attributes
Pathologic Processes
Gram-Negative Bacterial Infections
Bacterial Infections
Aztreonam
Anti-Bacterial Agents
Anti-Infective Agents
Therapeutic Uses
Pharmacologic Actions

ClinicalTrials.gov processed this record on May 23, 2013