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Found 6 studies with search of: Werdnig-Hoffman Disease
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Rank Status Study
1 Terminated
Has Results 		Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type I
Condition: Spinal Muscular Atrophy Type I
Intervention: Drug: sodium phenylbutyrate
2 Completed A Pilot Therapeutic Trial Using Hydroxyurea in Type I Spinal Muscular Atrophy Patients
Condition: Muscular Atrophy, Spinal
Intervention: Drug: Hydroxyurea
3 Recruiting Infants With Spinal Muscular Atrophy Type I
Condition: Spinal Muscular Atrophy
Intervention:
4 Active, not recruiting CARNIVAL Type I: Valproic Acid and Carnitine in Infants With Spinal Muscular Atrophy (SMA) Type I
Condition: Spinal Muscular Atrophy Type I
Intervention: Drug: Valproic Acid and Levocarnitine
5 Recruiting International SMA Patient Registry
Condition: Muscular Atrophy, Spinal
Intervention:
6 Completed A Pilot Study of Biomarkers for Spinal Muscular Atrophy
Condition: Spinal Muscular Atrophy
Intervention:

† Indicates status has not been verified in more than two years
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