Now Available for Public Comment: Notice of Proposed Rulemaking (NPRM) for FDAAA 801 and NIH Draft Reporting Policy for NIH-Funded Trials
2 studies found for:    16763906 [PUBMED-IDS]
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Rank Status Study
1 Active, not recruiting EPI-743 in Cobalamin C Defect: Effects on Visual and Neurological Impairment
Conditions: Methylmalonic Aciduria and Homocystinuria,Cblc Type;   Genetic Disease;   Retinopathy
Interventions: Drug: Epi-743;   Other: Placebo supplementation
2 Unknown  Anaplerotic Therapy in Propionic Acidemia
Condition: Propionic Acidemia
Interventions: Dietary Supplement: ornithine alpha ketoglutarate;   Dietary Supplement: glutamine;   Dietary Supplement: disodium citrate

Indicates status has not been verified in more than two years