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Found 54 studies with search of: Open Studies | "Thalassemia"
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Rank Status Study
1 Recruiting Prevalence of Pulmonary Hypertension (PAH) in Patients With Thalassemia
Conditions: Thalassemia Major;   Thalassemia Intermedia;   Pulmonary Arterial Hypertension
Intervention: Other: Physician standard-of-care according to ESC/ERS Guidelines
2 Recruiting Beta-thalassemia and Microparticles
Conditions: Thalassemia Major (TM);   Thalassemia Intermedia (TI);   Microparticles (MP)Originating From Platelets, Endothelial Cells and Monocytes
Intervention: Other: Physiopathology
3 Recruiting Stem Cell Transplant in Patients With Thalassemia
Condition: Thalassemia
Interventions: Drug: Busulfan;   Drug: Fludarabine;   Drug: Campath 1H;   Drug: Cyclophosphamide;   Drug: MESNA;   Procedure: Bone marrow or stem cell infusion
4 Recruiting Study to Determine the Safety and Tolerability of Sotatercept (ACE-011) in Adults With Red Blood Cell (RBC) Transfusion-dependent Beta-thalassemia (β Thalassemia)
Condition: Red Blood Cell (RBC) Transfusion-dependent Beta-Thalassemia
Intervention: Drug: SOTATERCEPT (ACE-011)
5 Unknown  Endocrine and Nutritional Assessment in B Thalassemia Major
Condition: Thalassemia
Intervention: Other: Nutritional recommendations
6 Recruiting Amlodipine in the Prevention and Treatment of Iron Overload in Patients With Thalassemia Major
Conditions: Thalassemia;   Iron Overload
Intervention: Drug: Amlodipine
7 Recruiting Stem Cell Transplant in Sickle Cell Disease and Thalassemia
Conditions: Sickle Cell Disease;   Beta Thalassemia
Interventions: Drug: Busulfan;   Drug: Fludarabine;   Drug: Alemtuzumab;   Procedure: Allogeneic stem cell transplant
8 Unknown  Iron Overload and Growth Velocity in Thalassemia and Sickle Cell Anemia
Conditions: Thalassemia;   Sickle Cell Disease
Intervention: Other: Medical Chart Summary
9 Not yet recruiting The Effect of Vitamin D Supplementation on Calcium Excretion in Thalassemia: a Dose Response Study
Condition: Thalassemia Major
Interventions: Drug: Vitamin D3;   Drug: Placebo
10 Recruiting Evaluating the Safety and Effectiveness of Mozobil Mobilization in Adults With Beta-Thalassemia Major
Condition: Beta-Thalassemia
Intervention: Drug: Mozobil
11 Unknown  Detection of β Thalassemia Carriers by Red Cell Parameters Obtained From the H2 Automatic Counter
Conditions: Thalassemia;   Iron Deficiency
Intervention: Procedure: Observation of results from laboratory tests
12 Unknown  The Change of Coagulation Markers in Children With β-Thalassemia Disease After Stem Cell Transplantation
Condition: Thalassemia
Intervention:
13 Recruiting Reduced Intensity Transplant Conditioning Regimen for Severe Thalassemia
Condition: Severe Thalassemia
Intervention: Drug: Transplant conditioning regimen of alemtuzumab, fludarabine, and melphalan
14 Recruiting Phase I Study to Examine the Effect of Deferasirox on Renal Hemodynamics in β-thalassemia Patients With Transfusional Iron Overload
Conditions: β-thalassemia;   Transfusional Iron Overload
Intervention: Drug: Deferasirox
15 Recruiting Genetic Factors Affecting the Severity of Beta Thalassemia
Condition: Beta Thalassemia
Intervention:
16 Unknown  Demographic, Clinical and Laboratory Characteristics of Children With Alpha Thalassemia in Northern Israel
Conditions: Thalassemia Alpha;   Hemolytic Anemia
Intervention: Other: Medical records summary
17 Recruiting Retroviral Vector Mediated Globin Gene Transfer to Correct Sickle Cell Anemia or Thalassemia
Conditions: Sickle Cell Anemia;   Thalassemia
Intervention: Genetic: Gene Therapy
18 Unknown  Factors Promoting Increased Rate and Success of Pregnancy in the Thalassemia Population in Toronto
Conditions: Thalassemia;   Fertility;   Pregnancy
Intervention:
19 Recruiting Safety and Efficacy of Deferasirox in β-thalassaemia Patients With Severe Cardiac Iron Overload
Conditions: Transfusion-dependent β-thalassemia Patients;   Cardiac Iron Overload
Interventions: Drug: Deferasirox;   Drug: Deferasirox + Deferoxamine
20 Recruiting A Phase III Safety and Efficacy Study of L-Glutamine to Treat Sickle Cell Disease or Sickle βo-thalassemia
Conditions: Sickle Cell Anemia;   Sickle ß0-Thalassemia
Interventions: Drug: L-glutamine;   Drug: 100% maltodextrin

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