A Study Of Inotuzumab Ozogamicin Versus Investigator's Choice Of Chemotherapy In Patients With Relapsed Or Refractory Acute Lymphoblastic Leukemia

This study is currently recruiting participants.
Verified June 2013 by Pfizer
Sponsor:
Collaborator:
Union Chimique Belge
Information provided by (Responsible Party):
Pfizer
ClinicalTrials.gov Identifier:
NCT01564784
First received: March 26, 2012
Last updated: June 3, 2013
Last verified: June 2013
  Purpose

This study will compare the efficacy, in terms of complete responses and overall survival, of inotuzumab ozogamicin versus investigator's choice of chemotherapy.


Condition Intervention Phase
Acute Lymphoblastic Leukemia
Drug: inotuzumab ozogamicin
Drug: FLAG (fludarabine, cytarabine and G-CSF)
Drug: HIDAC (high dose cytarabine)
Drug: cytarabine and mitoxantrone
Phase 3

Study Type: Interventional
Study Design: Allocation: Randomized
Endpoint Classification: Efficacy Study
Intervention Model: Parallel Assignment
Masking: Open Label
Primary Purpose: Treatment
Official Title: An Open-Label, Randomized Phase 3 Study Of Inotuzumab Ozogamicin Compared To A Defined Investigator's Choice In Adult Patients With Relapsed Or Refractory CD22-Positive Acute Lymphoblastic Leukemia (ALL)

Resource links provided by NLM:


Further study details as provided by Pfizer:

Primary Outcome Measures:
  • Response to therapy (percentage of patients achieving a complete response and complete response with incomplete platelet and/or neutrophil recovery). [ Time Frame: 6 months ] [ Designated as safety issue: No ]

Secondary Outcome Measures:
  • Overall Survival [ Time Frame: Baseline to 24 months ] [ Designated as safety issue: No ]
  • Progression free survival [ Time Frame: Baseline to 24 months ] [ Designated as safety issue: No ]
  • Volume of distribution (Vd) for inotuzumab ozogamicin in serum [ Time Frame: Cycle 1, Days 1, 3, 8 and 15; Cycle 2 , Days 1 and 8; Cycle 4, Days 1 and 8 ] [ Designated as safety issue: No ]
  • Systemic clearance (CL) for inotuzumab ozogamicin in serum [ Time Frame: Cycle 1, Days 1, 3, 8 and 15; Cycle 2 , Days 1 and 8; Cycle 4, Days 1 and 8 ] [ Designated as safety issue: No ]
  • Duration of response [ Time Frame: Baseline to 24 months ] [ Designated as safety issue: No ]
  • Rate of stem-cell transplantation: percentage of patients having stem-cell transplant [ Time Frame: Baseline to 8 months ] [ Designated as safety issue: No ]
  • Minimal residual disease (MRD): number of leukemic cells in bone marrow after CR/CRi [ Time Frame: Baseline to 7 months ] [ Designated as safety issue: No ]
  • Cytogenetics: quantitate t(9;22), MLL, and IGH rearrangements in leukemia cells [ Time Frame: Baseline to 7 months ] [ Designated as safety issue: No ]
  • Quality of life: . EORTC QLQ-C30 = European Organization for Research and Treatment of Cancer. Quality of Life Questionnaire, Core-30 [ Time Frame: Baseline to 6 months ] [ Designated as safety issue: No ]
  • Quality of life: EQ-5D = EuroQual -5D Health Questionnaire [ Time Frame: Baseline to 6 months ] [ Designated as safety issue: No ]

Estimated Enrollment: 292
Study Start Date: August 2012
Estimated Study Completion Date: March 2015
Estimated Primary Completion Date: June 2014 (Final data collection date for primary outcome measure)
Arms Assigned Interventions
Experimental: Arm A Drug: inotuzumab ozogamicin
Dose: inotuzumab ozogamicin 0.8-0.5 mg/m^2 IV, weekly, 3 times per cycle Cycle length: 21-28 days Total number of cycles: 6
Active Comparator: Arm B Drug: FLAG (fludarabine, cytarabine and G-CSF)
Dose: cytarabine 2.0 g/m^2/day IV days 1-6 fludarabine30 mg/m^2/day IV days 2-6 Cycle length: 28 days Total number of cycles: 4
Drug: HIDAC (high dose cytarabine)
cytarabine 3 g/m^2 IV every 12 hours for up to 12 times
Drug: cytarabine and mitoxantrone
mitoxantrone 12 mg/m^2 IV days 1-3 cytarabine 200 mg/m^2/day IV over 7 days cycle length: 15-20 days Total number of cycles: 4

  Eligibility

Ages Eligible for Study:   18 Years and older
Genders Eligible for Study:   Both
Accepts Healthy Volunteers:   No
Criteria

Inclusion Criteria:

  • CD22 expression
  • Adequate liver and renal functions

Exclusion Criteria:

  • Isolated extramedullary disease
  • Active Central Nervous System [CNS] disease
  Contacts and Locations
Please refer to this study by its ClinicalTrials.gov identifier: NCT01564784

Contacts
Contact: Pfizer CT.gov Call Center 1-800-718-1021

  Hide Study Locations
Locations
United States, California
Pfizer Investigational Site Recruiting
Los Angeles, California, United States, 90027
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Stanford, California, United States, 94305
United States, Colorado
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Aurora, Colorado, United States, 80045
United States, Florida
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Orlando, Florida, United States, 32806
United States, Georgia
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Atlanta, Georgia, United States, 30342
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Atlanta, Georgia, United States, 30322
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Augusta, Georgia, United States, 30912
United States, Illinois
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Chicago, Illinois, United States, 60611
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Chicago, Illinois, United States, 60637
United States, Kansas
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Kansas City, Kansas, United States, 66160
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Westwood, Kansas, United States, 66205
United States, Maryland
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Baltimore, Maryland, United States, 21287
United States, Massachusetts
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Boston, Massachusetts, United States, 02215
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Boston, Massachusetts, United States, 02115
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Boston, Massachusetts, United States, 02114
United States, Michigan
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Ann Arbor, Michigan, United States, 48109
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Detroit, Michigan, United States, 48201
United States, New Jersey
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Hackensack, New Jersey, United States, 07601
United States, New Mexico
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Albuquerque, New Mexico, United States, 87106
United States, New York
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Lake Success, New York, United States, 11042
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Manhasset, New York, United States, 11030
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New York, New York, United States, 10065
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New York, New York, United States, 10021
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Stony Brook, New York, United States, 11794
United States, Ohio
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Cleveland, Ohio, United States, 44106
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Cleveland, Ohio, United States, 44195
United States, Pennsylvania
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Hershey, Pennsylvania, United States, 17033
United States, South Carolina
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Easley, South Carolina, United States, 29640
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Greenville, South Carolina, United States, 29615
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Greenville, South Carolina, United States, 29605
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Greer, South Carolina, United States, 29650
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Seneca, South Carolina, United States, 29672
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Spartanburg, South Carolina, United States, 29307
United States, Texas
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Dallas, Texas, United States, 75246
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Houston, Texas, United States, 77030
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Laredo, Texas, United States, 78041
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San Antonio, Texas, United States, 78229
United States, Utah
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Salt Lake City, Utah, United States, 84103
United States, West Virginia
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Morgantown, West Virginia, United States, 26506
Australia, Victoria
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Box Hill, Victoria, Australia, 3128
Canada, Ontario
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Toronto, Ontario, Canada, M5G 2M9
Croatia
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Zagreb, Croatia, 10000
Czech Republic
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Prague, CZ, Czech Republic, 100-34
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Bmo, Czech Republic, 62500
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Hradec Kralove, Czech Republic, 50005
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Olomouc, Czech Republic, 77520
Finland
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Helsinki, Finland, 00290
France
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Le Chesnay, France, 78157
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Marseille, France, 13009
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Paris CEDEX 10, France, 75475
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Toulouse, Cedex 9, France, 31059
Germany
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Kiel, Germany, 24116
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Muenchen, Germany, 81675
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Muenster, Germany, 48149
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Oldenburg, Germany, 26133
Hungary
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Budapest, Hungary, 1097
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Debrecen, Hungary, 4032
Italy
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Bologna, Italy, 40138
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Catania, Italy
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Genova, Italy, 16132
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Monza, Italy, 20052
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Udine, Italy, 33100
Japan
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Sendai, Miyagi, Japan
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Chuo-ku, Tokyo, Japan
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Itabashi, Tokyo, Japan
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Koto-Ku, Tokyo, Japan
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Aichi, Japan
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Akita, Japan
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Fukuoka, Japan
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Hyogo, Japan
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Kanagawa, Japan
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Tokyo, Japan
Korea, Republic of
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Hwasun-Gun, Jeonnam, Korea, Republic of, 519-763
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Busan, Korea, Republic of, 614-735
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Incheon, Korea, Republic of, 405-760
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Seoul, Korea, Republic of, 135 710
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Seoul, Korea, Republic of, 110 744
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Seoul, Korea, Republic of, 137-701
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Seoul, Korea, Republic of, 138-736
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Seoul, Korea, Republic of, 140-743
Poland
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Warsaw, Poland, 02-776
Singapore
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Singapore, Singapore, 169608
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Singapore, Singapore, 119074
Slovakia
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Bratislava, Slovakia, 851 07
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Kosice, Slovakia, 041 66
Spain
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Badalona, Barcelona, Spain, 08916
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L'Hospitalet de Llobregat, Barcelona, Spain, 08908
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Barcelona, Catalunya, Spain, 00
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Palma de Mallorca, Illes Balears, Spain, 07198
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Barcelona, Spain
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Madrid, Spain, 28007
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Madrid, Spain, 28041
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Madrid, Spain
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Madrid, Spain, 28046
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Murcia, Spain, 30008
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Salamanca, Spain
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Sevilla, Spain, 41013
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Valencia, Spain, 46010
Sweden
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Lund, Sweden, 221 85
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Stockholm, Sweden, 171 76
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Uppsala, Sweden, 751 85
Taiwan
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Kaohsiung, Taiwan, 83301
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Taichung, Taiwan, 40705
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Taipei, Taiwan, 100
United Kingdom
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Oxford, Oxon, United Kingdom, OX3 7LJ
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Bristol, United Kingdom, BS2 8BJ
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Bristol, United Kingdom, BS2 8ED
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London, United Kingdom, NW3 2QG
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Manchester, United Kingdom, M20 4BX
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NorthHumberside, United Kingdom, Hu16 5JQ
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Southampton, United Kingdom, SO16 6YD
Sponsors and Collaborators
Pfizer
Union Chimique Belge
Investigators
Study Director: Pfizer CT.gov Call Center Pfizer
  More Information

Additional Information:
No publications provided

Responsible Party: Pfizer
ClinicalTrials.gov Identifier: NCT01564784     History of Changes
Other Study ID Numbers: B1931022
Study First Received: March 26, 2012
Last Updated: June 3, 2013
Health Authority: United States: Food and Drug Administration

Additional relevant MeSH terms:
Leukemia
Leukemia, Lymphoid
Precursor Cell Lymphoblastic Leukemia-Lymphoma
Neoplasms by Histologic Type
Neoplasms
Lymphoproliferative Disorders
Lymphatic Diseases
Immunoproliferative Disorders
Immune System Diseases
Cytarabine
Fludarabine monophosphate
Fludarabine
Mitoxantrone
Antimetabolites, Antineoplastic
Antimetabolites
Molecular Mechanisms of Pharmacological Action
Pharmacologic Actions
Antineoplastic Agents
Therapeutic Uses
Antiviral Agents
Anti-Infective Agents
Immunosuppressive Agents
Immunologic Factors
Physiological Effects of Drugs
Analgesics
Sensory System Agents
Peripheral Nervous System Agents
Central Nervous System Agents

ClinicalTrials.gov processed this record on June 18, 2013