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Pharmacokinetics and Tolerability of Zavesca® (Miglustat) In Patients With Juvenile GM2 Gangliosidosis

This study is ongoing, but not recruiting participants.
Study NCT00418847.   Last updated on January 4, 2007.   Information provided by The Hospital for Sick Children

Find Related Studies by Searching for the Conditions, Interventions, and Sponsors found in this study:
1 Conditions listed in this trial
Gangliosidoses GM2
2 Additional conditions recognized in this trial
Gangliosidoses
Gangliosidoses, GM2
Tay-Sachs Disease
3 More general conditions related to this trial
Brain Diseases
Brain Diseases, Metabolic
Brain Diseases, Metabolic, Inborn
Central Nervous System Diseases
Genetic Diseases, Inborn
Lipid Metabolism Disorders
Lipid Metabolism, Inborn Errors
Lipidoses
Lysosomal Storage Diseases
Lysosomal Storage Diseases, Nervous System
Metabolic Diseases
Metabolism, Inborn Errors
Nervous System Diseases
Sphingolipidoses
4 Interventions listed in this trial
miglustat
5 More general drug interventions related to this trial
Anti-HIV Agents
Anti-Infective Agents
Anti-Retroviral Agents
Antiviral Agents
Enzyme Inhibitors
Molecular Mechanisms of Pharmacological Action
Pharmacologic Actions
Therapeutic Uses
6 Sponsors listed in this trial
The Hospital for Sick Children
Actelion




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