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Metazym for the Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD)

This study is ongoing, but not recruiting participants.
Information provided by Zymenex A/S

Find Related Studies by Searching for the Conditions, Interventions, and Sponsors found in this study:
1 Conditions listed in this trial
Metachromatic Leukodystrophy
2 Additional conditions recognized in this trial
Leukodystrophy, Metachromatic
3 More general conditions related to this trial
Brain Diseases
Brain Diseases, Metabolic
Brain Diseases, Metabolic, Inborn
Central Nervous System Diseases
Congenital, Hereditary, and Neonatal Diseases and Abnormalities
Demyelinating Diseases
Genetic Diseases, Inborn
Hereditary Central Nervous System Demyelinating Diseases
Lipid Metabolism Disorders
Lipid Metabolism, Inborn Errors
Lipidoses
Lysosomal Storage Diseases
Lysosomal Storage Diseases, Nervous System
Metabolic Diseases
Metabolism, Inborn Errors
Nervous System Diseases
Nutritional and Metabolic Diseases
Sphingolipidoses
Sulfatidosis
4 Interventions listed in this trial
Metazym
5 Sponsors listed in this trial
Zymenex A/S