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5-Azacytidine and Phenylbutyrate to Treat Severe Thalassemia
This study has been completed.
Study NCT00005934 Information provided by National Institutes of Health Clinical Center (CC)
First Received: July 6, 2000 Last Updated: March 3, 2008
History of Changes
Related Studies can be found by searching for the Conditions, Interventions, and Sponsors found in this study:
Conditions listed in this trial
Beta Thalassemia
Additional conditions recognized in this trial
Beta-Thalassemia
Thalassemia
More general conditions related to this trial
Anemia
Anemia, Hemolytic
Anemia, Hemolytic, Congenital
Genetic Diseases, Inborn
Hematologic Diseases
Hemoglobinopathies
Interventions listed in this trial
5-Azacytidine
Additional drug interventions recognized in this trial
4-phenylbutyric acid
Azacitidine
More general drug interventions related to this trial
Antimetabolites
Antimetabolites, Antineoplastic
Antineoplastic Agents
Enzyme Inhibitors
Molecular Mechanisms of Pharmacological Action
Pharmacologic Actions
Therapeutic Uses
Sponsors listed in this trial
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
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