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Phase II Pilot Study of Granulocyte Colony-Stimulating Factor for Inherited Bone Marrow Failure Syndromes
This study has been completed.
Study NCT00004787 Information provided by Office of Rare Diseases (ORD)
First Received: February 24, 2000 Last Updated: June 23, 2005
History of Changes
Related Studies can be found by searching for the Conditions, Interventions, and Sponsors found in this study:
Conditions listed in this trial
Shwachman Syndrome
Fanconi's Anemia
Dyskeratosis Congenita
Thrombocytopenia
Additional conditions recognized in this trial
Anemia
Fanconi Anemia
Syndrome
More general conditions related to this trial
Anemia, Aplastic
Anemia, Hypoplastic, Congenital
Blood Platelet Disorders
Bone Marrow Diseases
Congenital Abnormalities
Disease
DNA Repair-Deficiency Disorders
Genetic Diseases, Inborn
Genetic Diseases, X-Linked
Hematologic Diseases
Metabolic Diseases
Pathologic Processes
Skin Abnormalities
Skin Diseases
Skin Diseases, Genetic
Interventions listed in this trial
filgrastim
Sponsors listed in this trial
National Center for Research Resources (NCRR)
James Whitcomb Riley Hospital for Children
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