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Phase I Study of Adenoviral Vector Mediated Gene Transfer for Ornithine Transcarbamylase in Adults With Partial Ornithine Transcarbamylase Deficiency

This study is ongoing, but not recruiting participants.
Study NCT00004498.   Last updated on June 23, 2005.   Information provided by FDA Office of Orphan Products Development

Find Related Studies by Searching for the Conditions, Interventions, and Sponsors found in this study:
1 Additional conditions recognized in this trial
Deficiency Diseases
Ornithine Carbamoyltransferase Deficiency Disease
2 More general conditions related to this trial
Amino Acid Metabolism, Inborn Errors
Brain Diseases
Brain Diseases, Metabolic
Brain Diseases, Metabolic, Inborn
Central Nervous System Diseases
Genetic Diseases, Inborn
Malnutrition
Metabolic Diseases
Metabolism, Inborn Errors
Nervous System Diseases
Nutrition Disorders
3 Sponsors listed in this trial
FDA Office of Orphan Products Development
University of Pennsylvania




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