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Phase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase Deficiency
This study has been terminated.
Study NCT00004386 Information provided by Office of Rare Diseases (ORD)
First Received: October 18, 1999 Last Updated: June 23, 2005
History of Changes
Related Studies can be found by searching for the Conditions, Interventions, and Sponsors found in this study:
Additional conditions recognized in this trial
Deficiency Diseases
Ornithine Carbamoyltransferase Deficiency Disease
More general conditions related to this trial
Amino Acid Metabolism, Inborn Errors
Brain Diseases
Brain Diseases, Metabolic
Brain Diseases, Metabolic, Inborn
Central Nervous System Diseases
Genetic Diseases, Inborn
Malnutrition
Metabolic Diseases
Metabolism, Inborn Errors
Nervous System Diseases
Nutrition Disorders
Sponsors listed in this trial
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
Children's Research Institute
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