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Stem Cell Transplantation (SCT) for Genetic Diseases
This study has been completed.
Study NCT00004378 Information provided by National Center for Research Resources (NCRR)
First Received: October 18, 1999 Last Updated: June 23, 2005
History of Changes
Related Studies can be found by searching for the Conditions, Interventions, and Sponsors found in this study:
Conditions listed in this trial
Thrombocytopenia
Metachromatic Leukodystrophy
Fanconi's Anemia
Thalassemia Major
Pure Red-Cell Aplasia
Inborn Errors of Metabolism
Additional conditions recognized in this trial
Anemia
Beta-Thalassemia
Fanconi Anemia
Leukodystrophy, Metachromatic
Metabolism, Inborn Errors
Red-Cell Aplasia, Pure
Thalassemia
More general conditions related to this trial
Anemia, Aplastic
Anemia, Hemolytic
Anemia, Hemolytic, Congenital
Anemia, Hypoplastic, Congenital
Blood Platelet Disorders
Bone Marrow Diseases
Brain Diseases
Brain Diseases, Metabolic
Brain Diseases, Metabolic, Inborn
Central Nervous System Diseases
Demyelinating Diseases
DNA Repair-Deficiency Disorders
Genetic Diseases, Inborn
Hematologic Diseases
Hemoglobinopathies
Hereditary Central Nervous System Demyelinating Diseases
Lipid Metabolism Disorders
Lipid Metabolism, Inborn Errors
Lipidoses
Lysosomal Storage Diseases
Lysosomal Storage Diseases, Nervous System
Metabolic Diseases
Nervous System Diseases
Sphingolipidoses
Sulfatidosis
Interventions listed in this trial
Stem Cell Transplantation
Sponsors listed in this trial
National Center for Research Resources (NCRR)
University of California, Los Angeles
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