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Phase II Pilot Study of Aminoimidazole Carboxamide Riboside (AICAR), a Precursor of Purine Synthesis, for Lesch-Nyhan Disease
This study has been completed.
Study NCT00004314 Information provided by Office of Rare Diseases (ORD)
First Received: October 18, 1999 Last Updated: June 23, 2005
History of Changes
Related Studies can be found by searching for the Conditions, Interventions, and Sponsors found in this study:
Conditions listed in this trial
Lesch-Nyhan Syndrome
Additional conditions recognized in this trial
Syndrome
More general conditions related to this trial
Brain Diseases
Brain Diseases, Metabolic
Brain Diseases, Metabolic, Inborn
Central Nervous System Diseases
Disease
Genetic Diseases, Inborn
Genetic Diseases, X-Linked
Heredodegenerative Disorders, Nervous System
Mental Retardation
Mental Retardation, X-Linked
Metabolic Diseases
Metabolism, Inborn Errors
Nervous System Diseases
Neurobehavioral Manifestations
Neurodegenerative Diseases
Neurologic Manifestations
Pathologic Processes
Purine-Pyrimidine Metabolism, Inborn Errors
Interventions listed in this trial
aminomidazole carboxamide riboside
Sponsors listed in this trial
National Center for Research Resources (NCRR)
University of California, San Diego
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