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Study to Evaluate the Safety of AT2220 in Pompe Disease

This study is currently recruiting participants.
Study NCT00688597.   Last updated on November 19, 2008.   Information provided by Amicus Therapeutics
Please refer to this study by its ClinicalTrials.gov identifier: NCT00688597


Locations
United States, Arizona
Phoenix Neurological Associates, LTD     Not yet recruiting
      Phoenix, Arizona, United States, 85006
      Contact: Lynne Flynn     602-258-2863     lynneflynn@pnal.net    
      Principal Investigator: Todd Levine, MD            
United States, California
Stanford University     Not yet recruiting
      Stanford, California, United States, 94305
      Contact: Gregory Enns, MD     650-498-5798     greg.enns@stanford.edu    
      Principal Investigator: Gregory Enns, MD, ChB            
University of California Irvine     Not yet recruiting
      Orange, California, United States, 92868
      Contact: Veronica Martin     714-456-2332        
      Principal Investigator: Tasheen Mozaffar, MD            
United States, Florida
University of Florida     Not yet recruiting
      Gainsville, Florida, United States, 32610-0296
      Contact: LeeAnn Lawson     352-273-7762     llawson@pedcard.ufl.edu    
      Principal Investigator: Barry Byrne, MD            
United States, Georgia
Emory University     Recruiting
      Decatur, Georgia, United States, 30033
      Contact: Eleanor Botha     404-778-8518        
      Principal Investigator: Paul Fernhoff, MD            
United States, Minnesota
University of Minnesota, Gene Therapy Center     Not yet recruiting
      Minneapolis, Minnesota, United States, 55455
      Contact: Jaan Schwake     612-624-8475     jschwake@umn.edu    
      Principal Investigator: Chester Whitley, MD, PhD            
United States, Missouri
Washington University of St. Louis     Not yet recruiting
      St. Louis, Missouri, United States, 63110
      Contact: Charlie Wulf     314-362-6980     wulfc@neuro.wustl.edu    
      Principal Investigator: Alan Pestronk, MD            
United States, New York
Center for Metabolic Disorders     Not yet recruiting
      Lake Success, New York, United States, 11042
      Contact: Linda Bulone     516-616-0074     bulonel@nychhc.org    
      Principal Investigator: Alfred Slonim            
United States, North Carolina
Duke University Medical Center     Not yet recruiting
      Durham, North Carolina, United States, 27710
      Contact: Joanne Mackey     919-681-1945     macke003@mc.duke.edu    
      Principal Investigator: Priya Kishnani, MD            
United States, Oregon
Oregon Health & Science University     Not yet recruiting
      Portland, Oregon, United States, 97239
      Contact: Eric Graf         grafe@OHSU.edu    
      Principal Investigator: Edward Cupler, MD            
United States, Pennsylvania
University of Pittsburgh     Not yet recruiting
      Pittsburgh, Pennsylvania, United States, 15238
      Contact: Paula Clemens, MD     412-648-9762        
      Principal Investigator: Paula Clemens, MD            
United States, Texas
Methodist Neurological Institute     Not yet recruiting
      Houston, Texas, United States, 77030
      Contact: Jessica Greene     713-441-3336     jgreene@tmhs.org    
      Principal Investigator: Ericka Simpson, MD            
United States, Washington
University of Washington     Not yet recruiting
      Seattle, Washington, United States, 98195-6490
      Contact: Phyllis Fluke     360-493-4272     phyllis.fluke@providence.org    
      Principal Investigator: Gregory Carter, MD            
Canada, Ontario
McMaster University Medical Center     Not yet recruiting
      Hamilton, Ontario, Canada, L8N3Z5
      Contact: Mark Tarnopolsky, MD, PhD     905-521-2100 ext 75226     taropol@mcmaster.ca    
      Principal Investigator: Mark Tarnopolsky, MD, PhD            
France
Hopital la Salpetriere     Not yet recruiting
      Paris, France, 75013
      Contact: Pascal Laforet, MD     33-1-42-163775     pascal.laforet@psl.ap-hop-paris.fr    
      Principal Investigator: Pascal Laforet, MD            
Germany
Neurologic Rehabilitation Centre Friedehorst     Not yet recruiting
      Bremen, Germany, D-28717
      Contact: Mattias Spranger, MD     49-421-6381501     spranger.nrz@friedehorst.de    
      Principal Investigator: Mattias Spranger, MD            
Ludwig Maximilians Universtiy Munich     Not yet recruiting
      Munchen, Germany, D-80336
      Contact: Benedikt Schoser, MD     4989-5160-7404-7443     bschoser@med.eni-muenchen.de    
      Principal Investigator: Benedikt Schoser, MD            
Netherlands
Erasmus MC Sophia Children's Hospital     Not yet recruiting
      Rotterdam, Netherlands, 3015
      Contact: Jacqueline Karelse     31-10 704 0 704        
      Principal Investigator: Ans van der Ploeg            
United Kingdom
Salford Royal NHS Trust Hope Hospital     Not yet recruiting
      Salford, United Kingdom, M68HD
      Contact: Marie Meehan     161-206-5151     marie.meehan@srht.nhs.uk    
      Principal Investigator: Stephen Waldek, MD            

Sponsors and Collaborators
Amicus Therapeutics

Investigators
Study Director:     Andrew Shenker, MD, PhD     Amicus Therapeutics    





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