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Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular Dystrophy

This study is currently recruiting participants.
Study NCT00159250.   Last updated on May 8, 2008.   Information provided by Imperial College London
Please refer to this study by its ClinicalTrials.gov identifier: NCT00159250


Contacts
Contact: Francesco Muntoni, FRCPCH     +442079052111     f.muntoni@imperial.ac.uk    
Contact: Kinali Maria, MRCPCH     + 44 2079052111     m.kinali@imperial.ac.uk    

Locations
United Kingdom
Dubowitz Neuromuscular Centre, Hammersmith Hospital and Clinical Trails Unit, St Mary's Hospital     Recruiting
      London, United Kingdom, W12 0HS
      Contact: Francesco Muntoni, FRCPCH     +44 20 7905 2111     f.muntoni@imperial.ac.uk    
      Contact: Maria Kinali, MRCPCH     +44 20 7905 2111        
      Principal Investigator: Francesco Muntoni, FRCPCH            
      Sub-Investigator: Mary Rutherford, FRCR            
      Sub-Investigator: Maria Kinali, MRCPCH            
      Sub-Investigator: Virginia Arechavala, PhD            
      Sub-Investigator: Caroline Sewry, PhD            
      Sub-Investigator: Lucy Feng, PhD            

Sponsors and Collaborators
Imperial College London
Department of Health

Investigators
Principal Investigator:     Francesco Muntoni, FRCPCH     Dubowitz neuromuscular Centre, Imperial College, London    
Study Director:     Kate Bushby, MRCP     Institute of Human Genetics, University of Newcastle upon Tyne    
Study Director:     Volker Straub, FRCPCH     Institute of Human Genetics, University of Newcastle upon Tyne    





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