Trial record 7 of 161 for:    Open Studies | "liver transplantation"

Efficacy, Safety and Tolerability of Everolimus in Combination With Reduced Exposure Cyclosporine or Tacrolimus in Paediatric Liver Transplant Recipients

This study is not yet open for participant recruitment.
Verified July 2012 by Novartis
Sponsor:
Information provided by (Responsible Party):
Novartis ( Novartis Pharmaceuticals )
ClinicalTrials.gov Identifier:
NCT01598987
First received: March 1, 2012
Last updated: July 31, 2012
Last verified: July 2012
  Purpose

This study is designed to assess the evolution of renal function and to collect efficacy, safety, and tolerability data of everolimus in co-exposure with reduced CNI in paediatric liver transplant recipients.


Condition Intervention Phase
Renal Function
Liver Transplant
Drug: Introduction of everolimus with reduced cyclosporine or tacrolimus dose, the earliest 1 month and the latest 6 months after liver transplantation.
Phase 3

Study Type: Interventional
Study Design: Endpoint Classification: Safety/Efficacy Study
Intervention Model: Single Group Assignment
Masking: Open Label
Primary Purpose: Treatment
Official Title: A 24-month, Multi-center, Single Arm, Prospective Study to Evaluate Renal Function, Efficacy, Safety and Tolerability of Everolimus in Combination With Reduced Exposure Cyclosporine or Tacrolimus in Paediatric Liver Transplant Recipients

Resource links provided by NLM:


Further study details as provided by Novartis:

Primary Outcome Measures:
  • Change in Glomerular Filtration Rate [ Time Frame: baseline, 12-month after start of study drug ] [ Designated as safety issue: No ]
    Renal function assessed by estimated Glomerular Filtration Rate 12-month after start of study drug.


Secondary Outcome Measures:
  • Rate of composite efficacy failure of treated biopsy proven acute rejection (tBPAR), graft loss (GL) or death (D). [ Time Frame: baseline, 12-month after start of study drug ] [ Designated as safety issue: No ]
    Efficacy failure rate of tBPAR, GL, or D.at 12-month after start of study drug

  • Number of Adverse Events [ Time Frame: baseline, 12-month and 24-month after start of study drug ] [ Designated as safety issue: Yes ]

    AE/SAEs as per preferred term and system organ class Incidence of treatment-related side effects Incidence and reason (e.g. AE) for premature discontinuation of study medication, and premature withdrawal from the study.

    Incidence and reason (e.g. AE) for dose interruption and dose adjustment of study medication.



Estimated Enrollment: 175
Study Start Date: July 2012
Estimated Primary Completion Date: October 2015 (Final data collection date for primary outcome measure)
Arms Assigned Interventions
Experimental: Everolimus based regimen
Conversion at Baseline from an immunosuppressive regimen which contains either cyclosporine (CsA) or tacrolimus (TAC) with or without mycophenolic acid (MPA), with or without corticosteroids in a regimen which contains everolimus combined reduced dose of either cyclosporine (CsA) or tacrolimus (TAC).
Drug: Introduction of everolimus with reduced cyclosporine or tacrolimus dose, the earliest 1 month and the latest 6 months after liver transplantation.
Immunosuppression after liver transplantation.

  Eligibility

Ages Eligible for Study:   1 Month to 17 Years
Genders Eligible for Study:   Both
Criteria

Key Inclusion Criteria:

  • Signed informed consent from both parents or legal guardian(s) prior to patient participation in the study.
  • Paediatric liver transplant recipients aged greater than or equal to 1 month and younger than 18 years of age.
  • Paediatric recipients at the earliest 1 month and latest 6 month after liver transplantation.

Key Exclusion Criteria:

  • Patients with hepato-biliary malignancies and/or patients transplanted due to fulminant hepatitis /acute liver failure.
  • Presence of thrombosis of any major hepatic arteries, major/reconstructed hepatic veins, portal vein or inferior vena cava at any time prior to the start of study drug.
  • Patients with serum creatinine value > 2 times age-related ULN at Baseline or who received renal replacement therapy within one week prior to the start of study drug and patients with a confirmed spot urine protein/creatinine ratio indicating a urinary protein excretion > 500 mg/m2/24 hrs, at Baseline.
  • Patients with clinically significant systemic infection and/or in a critical care setting requiring life support measures such as mechanical ventilation, dialysis, or vasopressor agents.
  • Patients with a known hypersensitivity to the drugs used on study or their class, or to any of the excipients.
  • Pregnant or nursing (lactating) female patients, where pregnancy is defined as the state of a female after conception and until the termination of gestation, confirmed by a positive βHCG laboratory test (> 9 mIU/mL) at Baseline.
  • Female patients of child-bearing potential, defined as all women physiologically capable of becoming pregnant, UNLESS they agree for abstinence from sexual activity.
  Contacts and Locations
No Contacts or Locations Provided
  More Information

No publications provided

Responsible Party: Novartis ( Novartis Pharmaceuticals )
ClinicalTrials.gov Identifier: NCT01598987     History of Changes
Other Study ID Numbers: CRAD001H2305, 2011-003069-14
Study First Received: March 1, 2012
Last Updated: July 31, 2012
Health Authority: United States: Food and Drug Administration

Keywords provided by Novartis:
Paediatric liver transplantation
Everolimus
Reduced calcineurin inhibitor
Cyclosporine, tacrolimus
Renal function
composite efficacy endpoint (biopsy proven acute rejection death, graft loss)

Additional relevant MeSH terms:
Cyclosporins
Cyclosporine
Everolimus
Sirolimus
Tacrolimus
Enzyme Inhibitors
Molecular Mechanisms of Pharmacological Action
Pharmacologic Actions
Immunosuppressive Agents
Immunologic Factors
Physiological Effects of Drugs
Antifungal Agents
Anti-Infective Agents
Therapeutic Uses
Dermatologic Agents
Antirheumatic Agents
Antibiotics, Antineoplastic
Antineoplastic Agents
Anti-Bacterial Agents

ClinicalTrials.gov processed this record on May 22, 2013