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A Phase I Study of LJM716 in Squamous Cell Carcinoma of Head and Neck, or HER2+ Breast Cancer or Gastric Cancer

This study is currently recruiting participants.
Verified May 2013 by Novartis
Sponsor:
Information provided by (Responsible Party):
Novartis ( Novartis Pharmaceuticals )
ClinicalTrials.gov Identifier:
NCT01598077
First received: May 4, 2012
Last updated: May 8, 2013
Last verified: May 2013
  Purpose

This primary purpose of this study is to estimate the maximum tolerated dose (MTD) and/or recommended dose for expansion (RDE) and preferred dosing schedule of LJM716 given by IV infusion in adult patients with squamous cell carcinoma of head and neck, or esophagus, or HER2 overexpressing metastatic breast cancer or gastric cancer


Condition Intervention Phase
HER2 + Breast Cancer, HER2 + Gastric Cancer, Squamous Cell Carcinoma of Head and Neck, Esophageal Squamous Cell Carcinoma
HER2 + Breast Cancer
HER2 + Gastric Cancer
Squamous Cell Carcinoma of Head and Neck
Esophageal Squamous Cell Carcinoma
Drug: LJM716
Phase 1

Study Type: Interventional
Study Design: Allocation: Non-Randomized
Endpoint Classification: Safety Study
Intervention Model: Single Group Assignment
Masking: Open Label
Primary Purpose: Treatment
Official Title: A Phase I Study of LJM716 in Patients With Squamous Cell Carcinoma of Head and Neck, or HER2 Overexpressing Metastatic Breast Cancer or Gastric Cancer

Resource links provided by NLM:


Further study details as provided by Novartis:

Primary Outcome Measures:
  • Dose-limiting toxicities (DLTs) [ Time Frame: 4 weeks ] [ Designated as safety issue: Yes ]

Secondary Outcome Measures:
  • Adverse events [ Time Frame: 4 months ] [ Designated as safety issue: Yes ]
  • Serious adverse events [ Time Frame: 4 months ] [ Designated as safety issue: Yes ]
  • Pharmacodynamic response to LJM716 in tumor tissue [ Time Frame: 3 months ] [ Designated as safety issue: No ]
  • Frequency of partial responses, complete responses and stable disease according to RECIST [ Time Frame: every 2 months ] [ Designated as safety issue: No ]
  • Serum concentration of antibodies to LJM716 [ Time Frame: 18 months ] [ Designated as safety issue: No ]
  • Progression-free survival [ Time Frame: 18 months ] [ Designated as safety issue: No ]
  • Duration of response [ Time Frame: 18 months ] [ Designated as safety issue: No ]
  • Serum concentration of LJM716, [ Time Frame: 4 months ] [ Designated as safety issue: No ]

Estimated Enrollment: 50
Study Start Date: July 2012
Estimated Study Completion Date: June 2014
Estimated Primary Completion Date: June 2014 (Final data collection date for primary outcome measure)
Arms Assigned Interventions
Experimental: Dose escalation and dose expansion Drug: LJM716

  Eligibility

Ages Eligible for Study:   18 Years and older
Genders Eligible for Study:   Both
Accepts Healthy Volunteers:   No
Criteria

Inclusion criteria:

  • Patients with HER2+ breast cancer, or HER2+ gastric cancer, or squamous cell carcinoma of head and neck, or esophageal squamous cell carcinoma
  • Site of disease that can be safely biopsied

Exclusion criteria:

  • Patients received prior anti-HER3 antibody treatment
  • Patients with impaired cardiac function
  • Brain metastases that have not been adequately treated
  • Malignant disease other than that being treated in this study
  • Pregnant or nursing (lactating) women
  • Laboratory abnormalities as specified in the protocol Other protocol-defined inclusion/exclusion criteria may apply
  Contacts and Locations
Please refer to this study by its ClinicalTrials.gov identifier: NCT01598077

Contacts
Contact: Novartis Pharmaceuticals 1-888-669-6682
Contact: Novartis Pharmaceuticals

Locations
United States, Illinois
University of Chicago Medical Center University of Chicago (16) Recruiting
Chicago, Illinois, United States, 60546
Contact: David Geary     773-702-2452     dgeary@medicine.bsd.uchicago.edu    
Principal Investigator: Ezra Cohen            
United States, Massachusetts
Massachusetts General Hospital SC-5 Recruiting
Boston, Massachusetts, United States, 02114
Contact: Rosemary Boyle         rboyle1@partners.org    
Principal Investigator: Dejan Juric            
United States, Texas
MD Anderson Cancer Center/University of Texas UT MD Recruiting
Houston, Texas, United States, 77030-4009
Contact: Sara Nasser     713-792-3391     snasser@mdanderson.org    
Principal Investigator: George Blumenschein            
United States, Utah
University of Utah / Huntsman Cancer Institute Huntsman Recruiting
Salt Lake City, Utah, United States, 84103
Contact: Danielle Tometich     801-585-0443     danielle.tometich@hci.utah.edu    
Principal Investigator: Ignacio Garrido-Laguna            
Canada, Ontario
Novartis Investigative Site Recruiting
Toronto, Ontario, Canada, M5G 2M9
Korea, Republic of
Novartis Investigative Site Recruiting
Seoul, Korea, Korea, Republic of, 110 744
Spain
Novartis Investigative Site Recruiting
Barcelona, Cataluna, Spain, 08035
Taiwan
Novartis Investigative Site Recruiting
Taipei, Taiwan, 10002
Sponsors and Collaborators
Novartis Pharmaceuticals
Investigators
Study Director: Novartis Pharmaceuticals Novartis Pharmaceuticals
  More Information

No publications provided

Responsible Party: Novartis ( Novartis Pharmaceuticals )
ClinicalTrials.gov Identifier: NCT01598077     History of Changes
Other Study ID Numbers: CLJM716X2101, 2011-004865-33
Study First Received: May 4, 2012
Last Updated: May 8, 2013
Health Authority: United States: Food and Drug Administration
Canada: Health Canada
Spain: Ministry of Health
Korea: Food and Drug Administration
Taiwan : Food and Drug Administration

Keywords provided by Novartis:
Breast cancer, gastric cancer, squamous cell carcinoma of head and neck, esophageal squamous cell carcinoma
Breast cancer
Gastric cancer
Squamous cell carcinoma of head and neck
Esophageal squamous cell carcinoma

Additional relevant MeSH terms:
Carcinoma
Carcinoma, Squamous Cell
Breast Neoplasms
Esophageal Diseases
Stomach Neoplasms
Neoplasms, Squamous Cell
Head and Neck Neoplasms
Neoplasms by Site
Neoplasms
Breast Diseases
Skin Diseases
Neoplasms, Glandular and Epithelial
Neoplasms by Histologic Type
Gastrointestinal Diseases
Digestive System Diseases
Gastrointestinal Neoplasms
Digestive System Neoplasms
Stomach Diseases

ClinicalTrials.gov processed this record on May 23, 2013