Efficacy of Everolimus in Combination With Tacrolimus in Liver Transplant Recipients (HEPHAISTOS)

This study is currently recruiting participants.
Verified January 2013 by Novartis
Sponsor:
Collaborator:
CROLLL, Winicker Norimed
Information provided by (Responsible Party):
Novartis ( Novartis Pharmaceuticals )
ClinicalTrials.gov Identifier:
NCT01551212
First received: March 8, 2012
Last updated: January 15, 2013
Last verified: January 2013
  Purpose

This trial will evaluate the efficacy of Everolimus in combination tacrolimus versus a standard immunosuppressive regimen concerning kidney function in liver transplant recipients.


Condition Intervention Phase
Liver Transplantation
Drug: Everolimus (RAD001) as add-on
Drug: tacrolimus group
Phase 3

Study Type: Interventional
Study Design: Allocation: Randomized
Intervention Model: Parallel Assignment
Masking: Open Label
Primary Purpose: Treatment
Official Title: A 12 Month, Multi-center, Open-label, Randomized, Controlled Study to Evaluate Efficacy/Safety and Evolution of Renal Function of Everolimus in Co-exposure With Tacrolimus in de Novo Liver Transplant Recipients

Resource links provided by NLM:


Further study details as provided by Novartis:

Primary Outcome Measures:
  • Estimated glomerular filtration rate (MDRD-4 formula) at Month 12 in de novo liver [ Time Frame: at 12 months after randomization ] [ Designated as safety issue: No ]
    Immunosuppressive regimen based on everolimus (EVR) in coexposure with tacrolimus (TAC) compared to tacrolimus alone on estimated glomerular filtration rate (MDRD-4 formula) at Month 12 in de novo liver transplant recipients.


Secondary Outcome Measures:
  • Incidence of composite of treated biopsy proven acute rejection (BPAR), graft loss or death [ Time Frame: 12 months after randomization ] [ Designated as safety issue: Yes ]
  • Incidence of HCV and HCV related fibrosis [ Time Frame: at 12 months after randomization ] [ Designated as safety issue: No ]
  • Incidence and severity of CMV viral infections. [ Time Frame: at 12 months after randomization ] [ Designated as safety issue: No ]
  • Incidence of de novo HCC malignancies [ Time Frame: at 12 weeks after randomization ] [ Designated as safety issue: No ]
  • Incidence of and response to HCV antiviral treatment [ Time Frame: at 12 months after randomization ] [ Designated as safety issue: No ]

Estimated Enrollment: 330
Study Start Date: May 2012
Estimated Primary Completion Date: April 2015 (Final data collection date for primary outcome measure)
Arms Assigned Interventions
Active Comparator: tacrolimus group
standby therapy
Drug: tacrolimus group
Experimental: tacrolimus minimization group
Everolimus (RAD001) as add-on
Drug: Everolimus (RAD001) as add-on

  Eligibility

Ages Eligible for Study:   18 Years to 65 Years
Genders Eligible for Study:   Both
Accepts Healthy Volunteers:   No
Criteria

Inclusion criteria:

  • Male or female recipients of a full-size liver allograft, aged 18 to 65 years.

Exclusion criteria:

  • Patients with thrombocytopenia (platelets <100,000/mm³), with an absolute neutrophil count of <1,500/mm³ or leucopenia (leucocytes <3000/mm³), with anemia with Hb < 8g/dl at time of screening
  • Patients with uncontrolled hypercholesterolemia (>330mg/dL; >9mmol/L) or hypertriglyceridemia (>300 mg/dL; >8.5 mmol/L) at time of screening
  • History of malignancy of any organ system within the past 5 years whether or not there is evidence of local recurrence or metastases, other than non-metastatic basal or squamous cell carcinoma of the skin or HCC (see next criteria).
  • Other protocol-defined inclusion/exclusion criteria may apply
  Contacts and Locations
Please refer to this study by its ClinicalTrials.gov identifier: NCT01551212

Locations
Germany
Novartis Investigational Site Recruiting
Berlin, Germany
Contact: Study Director     +41-61-324-1111        
Novartis Investigational Site Recruiting
Essen, Germany
Contact: Study Director     +41-61-324-1111        
Novartis Investigational Site Recruiting
Großhadern, Germany
Contact: Study Director     +41-61-324-1111        
Novartis Investigational Site Recruiting
Hamburg, Germany
Contact: Study Director     +41-61-324-1111        
Novartis Investigational Site Not yet recruiting
Hannover, Germany
Contact: Stduy Director     +41-61-324-1111        
Novartis Investigational Site Not yet recruiting
Leipzig, Germany
Contact: Study Director     +41-61-324-1111        
Novartis Investigational Site Recruiting
Mainz, Germany
Contact: Study Director     +41-61-324-1111        
Sponsors and Collaborators
Novartis Pharmaceuticals
CROLLL, Winicker Norimed
  More Information

No publications provided

Responsible Party: Novartis ( Novartis Pharmaceuticals )
ClinicalTrials.gov Identifier: NCT01551212     History of Changes
Other Study ID Numbers: CRAD001HDE13, 2011-003118-17
Study First Received: March 8, 2012
Last Updated: January 15, 2013
Health Authority: United States: Institutional Review Board
Germany: Federal Institute for Drugs and Medical Devices

Keywords provided by Novartis:
Liver transplantation
everolimus
kidney function

Additional relevant MeSH terms:
Everolimus
Sirolimus
Tacrolimus
Immunosuppressive Agents
Immunologic Factors
Physiological Effects of Drugs
Pharmacologic Actions
Antibiotics, Antineoplastic
Antineoplastic Agents
Therapeutic Uses
Antifungal Agents
Anti-Infective Agents
Anti-Bacterial Agents

ClinicalTrials.gov processed this record on May 16, 2013