Research of Biomarkers in Duchenne Muscular Dystrophy Patients (IBISD)
The purpose of this study is to identify potential biomarkers for the diagnosis, disease progression assessment and response to treatment in patients with Duchenne Muscular Dystrophy.
Duchenne Muscular Dystrophy (DMD)
|Study Design:||Observational Model: Cohort
Time Perspective: Prospective
|Official Title:||Research of Biomarkers for Disease Diagnosis, Disease Monitoring and Therapeutic Treatment Response in Duchenne Muscular Dystrophy Patients|
- IBiSD aims to identify and validate new and disease-specific biomarkers. [ Time Frame: End of study ] [ Designated as safety issue: No ]This study will establish the relevance of urinary and blood biomarkers for the diagnosis, follow-up and assessment of treatment response in patients with DMD (IBiSD1, 2 and 4). IBiSD will also attempt to establish the seroprevalence to the different strains of AAV in patients with DMD (IBiSD3).
Biospecimen Retention: Samples With DNA
DNA, serum, t lymphocytes, urine
|Study Start Date:||June 2011|
|Estimated Study Completion Date:||December 2015|
|Estimated Primary Completion Date:||December 2015 (Final data collection date for primary outcome measure)|
|Institute of Myology||Recruiting|
|Contact: Laurent Servais, MD +33(0)142169966 firstname.lastname@example.org|
|Principal Investigator: Laurent Servais, MD|
|Principal Investigator:||Laurent SERVAIS, MD||Myology Institute|