Universal GM-CSF-Producing and GM.CD40L for Autologous Tumor Vaccine in Mantle Cell Lymphoma

This study is ongoing, but not recruiting participants.
Sponsor:
Collaborators:
Lymphoma Research Foundation
Novartis
Information provided by (Responsible Party):
H. Lee Moffitt Cancer Center and Research Institute
ClinicalTrials.gov Identifier:
NCT00101101
First received: January 7, 2005
Last updated: February 12, 2013
Last verified: February 2013
  Purpose

RATIONALE: Vaccines made from gene-modified cells and a person's cancer cells may make the body build an effective immune response to kill cancer cells. Interleukin-2 (IL-2) may stimulate the white blood cells to kill cancer cells. Giving booster vaccinations may make a stronger immune response and prevent or delay the recurrence of cancer. Drugs used in chemotherapy work in different ways to stop the growth of cancer cells, either by killing the cells or by stopping them from dividing. Giving more than one drug (combination chemotherapy) may kill more cancer cells. Giving vaccine therapy together with IL-2 after combination chemotherapy may be a more effective treatment for mantle cell lymphoma.

PURPOSE: This phase II trial is studying how well giving vaccine therapy together with IL-2 after combination chemotherapy works in treating patients with relapsed or de novo stage II, stage III, or stage IV mantle cell lymphoma.


Condition Intervention Phase
Lymphoma
Drug: Cyclophosphamide, Hyperfractionated Cyclophosphamide
Drug: Doxorubicin
Drug: Vincristine
Drug: Prednisone
Drug: Dexamethasone
Drug: High-Dose Methotrexate
Biological: Autologous Tumor Cell-Based Vaccine
Drug: IL-2
Phase 2

Study Type: Interventional
Study Design: Endpoint Classification: Safety/Efficacy Study
Intervention Model: Single Group Assignment
Masking: Open Label
Primary Purpose: Treatment
Official Title: A Phase II Trial Using a Universal GM-CSF-Producing and CD40L-Expressing Bystander Cell Line (GM.CD40L) in the Formulation of Autologous Tumor Cell-Based Vaccines for Patients With Mantle Cell Lymphoma

Resource links provided by NLM:


Further study details as provided by H. Lee Moffitt Cancer Center and Research Institute:

Primary Outcome Measures:
  • Number of Participants With Anti-Tumor Response [ Time Frame: 6 years ] [ Designated as safety issue: No ]
    To evaluate patients for the development of specific anti-tumor immune responses after immunization with the autologous tumor cell / GM.CD40L bystander cell vaccine. Immunogenicity will be measured by in vitro testing of peripheral blood lymphocytes (PBLs) for cytokine-secreting T cells in enzyme-linked immunospot (ELISPOT) assays, delayed-type hypersensitivity (DTH) skin testing with irradiated autologous tumor cells, and biopsy of the DTH site for immunohistochemical analysis of infiltrating lymphocytes 48 hours after intradermal injection of autologous tumor cells. Vaccine injection sites will be biopsied to evaluate local response to vaccination.


Secondary Outcome Measures:
  • Frequency of Toxicity Related to Study Treatment [ Time Frame: 6 years ] [ Designated as safety issue: Yes ]
    To evaluate the toxicity of the autologous tumor cell / GM.CD40L bystander cell vaccine. Review of adverse events utilizing Common Toxicity Criteria (CTC) V3.


Enrollment: 43
Study Start Date: July 2004
Estimated Study Completion Date: August 2013
Estimated Primary Completion Date: August 2013 (Final data collection date for primary outcome measure)
Arms Assigned Interventions
Experimental: Conventional Chemotherapy and Vaccine Therapy

Conventional chemotherapy: Patients receive conventional chemotherapy comprising 6 courses of cyclophosphamide, doxorubicin, vincristine, and prednisone (CHOP) OR 3 courses of hyperfractionated cyclophosphamide, vincristine, doxorubicin, and dexamethasone alternating with high-dose methotrexate and cytarabine (hyper-CVAD) for patients who have relapsed after CHOP. Patients who achieve a partial or complete response after completion of chemotherapy proceed to vaccine therapy.

Vaccine therapy: Patients receive vaccine comprising autologous tumor cells and GM.CD40L intradermally on day 1 and low-dose interleukin-2 (IL-2) subcutaneously twice daily on days 1-14. Treatment repeats every 28 days for 4 courses. Patients who have stable or responding disease at 12 months receive 4 additional courses of booster vaccine and low-dose IL-2 as above. Treatment continues in the absence of disease progression or unacceptable toxicity.

Drug: Cyclophosphamide, Hyperfractionated Cyclophosphamide
Other Name: Cytoxan
Drug: Doxorubicin
Other Names:
  • adriamycin
  • Rubex
Drug: Vincristine
Other Names:
  • Oncovin
  • leurocristine
  • VCR
Drug: Prednisone
Other Names:
  • Deltasone
  • Liquid Pred
  • Meticorten
  • Orasone
Drug: Dexamethasone
Other Names:
  • Decadron
  • Dexasone
  • Diodex
  • Hexadrol
Drug: High-Dose Methotrexate
Other Names:
  • Rheumatrex
  • Trexall
Biological: Autologous Tumor Cell-Based Vaccine
A therapeutic agent produced by isolating tumor cells from an individual and processing these tumor cells into a vaccine formulation in vitro; the vaccine is then administered to the individual from whom the tumor cells were isolated.
Drug: IL-2
Other Names:
  • interleukin-2
  • cytokine
  • aldesleukin

Detailed Description:

OBJECTIVES:

Primary

  • Determine the specific anti-tumor immune response in patients with relapsed or de novo stage II, III, or IV mantle cell lymphoma treated with vaccine therapy comprising autologous tumor cells and a sargramostim (GM-CSF)-producing and CD40L-expressing cell line (GM.CD40L) combined with low-dose interleukin-2 after conventional chemotherapy.
  • Determine the toxicity of this regimen in these patients.

Secondary

  • Determine the tumor response rate, time to progression, disease-free survival, and overall survival of patients treated with this regimen.

OUTLINE: Patients undergo surgical resection of a malignant lymph node to collect autologous tumor cells for vaccine production. Vaccine is formulated by combining equal volumes of irradiated autologous tumor cells and irradiated cells from a cell line that produces sargramostim (GM-CSF) and expresses CD40L (GM.CD40L).

  • Conventional chemotherapy: Patients receive conventional chemotherapy comprising 6 courses of cyclophosphamide, doxorubicin, vincristine, and prednisone (CHOP) OR 3 courses of hyperfractionated cyclophosphamide, vincristine, doxorubicin, and dexamethasone alternating with high-dose methotrexate and cytarabine (hyper-CVAD) for patients who have relapsed after CHOP. Patients who achieve a partial or complete response after completion of chemotherapy proceed to vaccine therapy.
  • Vaccine therapy: Patients receive vaccine comprising autologous tumor cells and GM.CD40L intradermally on day 1 and low-dose interleukin-2 (IL-2) subcutaneously twice daily on days 1-14. Treatment repeats every 28 days for 4 courses. Patients who have stable or responding disease at 12 months receive 4 additional courses of booster vaccine and low-dose IL-2 as above. Treatment continues in the absence of disease progression or unacceptable toxicity.

Patients are followed every 3 months until disease progression and then annually thereafter.

PROJECTED ACCRUAL: A total of 40-60 patients will be accrued for this study within 15 months.

  Eligibility

Ages Eligible for Study:   18 Years and older
Genders Eligible for Study:   Both
Accepts Healthy Volunteers:   No
Criteria

DISEASE CHARACTERISTICS:

  • Histologically confirmed mantle cell lymphoma

    • Stage II, III, or IV disease
    • Relapsed or de novo disease
  • No symptomatic brain metastasis

PATIENT CHARACTERISTICS:

Age

  • 18 and over

Performance status

  • Eastern Cooperative Oncology Group (ECOG) 0-2

Life expectancy

  • Not specified

Hematopoietic

  • White blood count (WBC) > 3,000/mm^3
  • Absolute neutrophil count > 1,500/mm^3
  • Platelet count > 100,000/mm^3
  • Hematocrit > 25%
  • Hemoglobin > 8 g/dL

Hepatic

  • Bilirubin < 2.0 mg/dL

Renal

  • Creatinine < 2.0 mg/dL OR
  • Creatinine clearance > 60 mL/min

Immunologic

  • No serious ongoing infection
  • No known HIV infection
  • No other pre-existing immunodeficiency condition

Other

  • Not pregnant or nursing
  • Negative pregnancy test
  • Fertile patients must use effective contraception for 1 month before, during, and for 3 months after study treatment

PRIOR CONCURRENT THERAPY:

Biologic therapy

  • No other concurrent immunotherapy

Chemotherapy

  • More than 4 weeks since prior chemotherapy
  • No other concurrent chemotherapy

Endocrine therapy

  • More than 4 weeks since prior steroids
  • No concurrent corticosteroids except as replacement doses in patients who are hypoadrenal

Radiotherapy

  • More than 2 weeks since prior radiotherapy
  • No concurrent radiotherapy

Surgery

  • Not specified

Other

  • No other concurrent immunosuppressive therapy
  Contacts and Locations
Please refer to this study by its ClinicalTrials.gov identifier: NCT00101101

Locations
United States, Florida
H. Lee Moffitt Cancer Center and Research Institute
Tampa, Florida, United States, 33612-9497
Sponsors and Collaborators
H. Lee Moffitt Cancer Center and Research Institute
Lymphoma Research Foundation
Novartis
Investigators
Principal Investigator: Sophie Dessureault, M.D., Ph.D. H. Lee Moffitt Cancer Center and Research Institute
  More Information

Additional Information:
No publications provided

Responsible Party: H. Lee Moffitt Cancer Center and Research Institute
ClinicalTrials.gov Identifier: NCT00101101     History of Changes
Other Study ID Numbers: MCC-13840, 0406-654
Study First Received: January 7, 2005
Last Updated: February 12, 2013
Health Authority: United States: Food and Drug Administration

Keywords provided by H. Lee Moffitt Cancer Center and Research Institute:
recurrent mantle cell lymphoma
contiguous stage II mantle cell lymphoma
noncontiguous stage II mantle cell lymphoma
stage III mantle cell lymphoma
stage IV mantle cell lymphoma

Additional relevant MeSH terms:
Lymphoma
Lymphoma, Mantle-Cell
Neoplasms by Histologic Type
Neoplasms
Lymphoproliferative Disorders
Lymphatic Diseases
Immunoproliferative Disorders
Immune System Diseases
Lymphoma, Non-Hodgkin
Cyclophosphamide
Methotrexate
Dexamethasone
Doxorubicin
Interleukin-2
Prednisone
Vincristine
Dexamethasone acetate
Dexamethasone 21-phosphate
BB 1101
Immunosuppressive Agents
Immunologic Factors
Physiological Effects of Drugs
Pharmacologic Actions
Antirheumatic Agents
Therapeutic Uses
Antineoplastic Agents, Alkylating
Alkylating Agents
Molecular Mechanisms of Pharmacological Action
Antineoplastic Agents
Myeloablative Agonists

ClinicalTrials.gov processed this record on May 21, 2013