RG2133 (2',3',5'-Tri-O-Acetyluridine) in Mitochondrial Disease
This study has been terminated.
Information provided by:
First received: May 7, 2003
Last updated: August 4, 2005
Last verified: August 2005
The objective of the study is to determine the safety and tolerability of RG2133 in patients with Mitochondrial Disease.
Drug: RG2133 (2',3',5'-tri-O-acetyluridine)
|Study Design:||Allocation: Non-Randomized
Primary Purpose: Treatment
|Official Title:||An Open-Label Dose-Escalation Phase I Study to Asses the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of RG2133 (2',3',5'-Tri-O-Acetyluridine) in the Treatment of Inherited Mitochondrial Diseases|
Resource links provided by NLM:
Genetics Home Reference related topics: ataxia neuropathy spectrum childhood myocerebrohepatopathy spectrum deoxyguanosine kinase deficiency mitochondrial neurogastrointestinal encephalopathy disease myoclonic epilepsy myopathy sensory ataxiaU.S. FDA Resources
Further study details as provided by Repligen Corporation:
Contacts and Locations
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