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Found 73 studies with search of: Hemophilia | Open Studies
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Rank Status Study
1 Recruiting Gene Transfer for Subjects With Hemophilia B Factor IX Deficiency
Condition: Hemophilia B
Intervention: Biological: AAV2-hFIX
2 Recruiting Study of Ataluren (PTC124™) in Hemophilia A and B
Conditions: Hemophilia A;   Hemophilia B
Intervention: Drug: Ataluren (PTC124)
3 Recruiting Females With Severe or Moderate Hemophilia A or B: an International Multi-center Study
Conditions: Hemophilia A;   Hemophilia B
Intervention:
4 Recruiting Rituximab to Treat Severe Hemophilia A
Condition: Hemophilia A
Intervention: Drug: Rituximab
5 Not yet recruiting Efficacy and Safety of MK-0518 in Treatment-Experienced HIV-1 Infected Adult Patients With Hemophilia
Conditions: HIV Infection;   Hemophilia A
Intervention:
6 Recruiting Efficacy and Safety Study of Prophylactic Versus On-Demand Treatment With Feiba NF in Subjects With Hemophilia A or B and a High Titer Inhibitor
Conditions: Hemophilia A;   Hemophilia B;   (High-titer) Factor VIII Inhibitor;   (High-titer) Factor IX Inhibitor
Intervention: Biological: Factor VIII Inhibitor Bypassing Activity (nanofiltered, vapor heat-treated)
7 Recruiting Study Evaluating Liver Transplantation in Haemophilia Patients in Spain
Conditions: Hemophilia A;   Hemophilia B
Intervention: Other: Non-interventional epidemiological study
8 Not yet recruiting Bleeding Symptoms of Carriers of Hemophilia A and B
Condition: Hemophilia
Intervention:
9 Recruiting Dose-Escalation Study Of A Self Complementary Adeno-Associated Viral Vector For Gene Transfer in Hemophilia B
Condition: Hemophilia B
Intervention: Genetic: Gene Transfer
10 Recruiting Study of a Recombinant Protein-Free Factor VIII (rAHF-PFM): Comparison of Continuous Infusion Versus Intermittent Bolus Infusion in Hemophilia A Subjects Undergoing Unilateral Knee Replacement
Condition: Hemophilia A
Intervention: Drug: Recombinant Protein-Free Factor VIII (rAHF-PFM)
11 Recruiting Safety Study of Alphanate in Previously Treated Patients With Severe Hemophilia A
Condition: Severe Hemophilia A
Intervention: Drug: Alphanate SD
12 Recruiting Post-marketing Safety Surveillance of NovoSeven® in Patients With Haemophilia and Inhibitors by Means of the UK Haemophilia Database
Conditions: Haemophilia A;   Haemophilia B
Intervention: Drug: activated recombinant human factor VII
13 Recruiting Study of a Plasma-derived Von Willebrand Factor/Factor VIII Concentrate (vWF/FVIII), Biostate®, in Subjects With Haemophilia A
Condition: Hemophilia A
Interventions: Biological: Biostate® [SP];   Biological: Biostate® [RP]
14 Recruiting Hemophilia Inhibitor Genetics Study (HIGS)
Condition: Hemophilia A With Inhibitor
Intervention: Procedure: Blood draw
15 Recruiting Study of Recombinant Factor VIII Fc Fusion Protein (rFVIIIFc) in Subjects With Severe Hemophilia A
Condition: Severe Hemophilia A
Intervention: Drug: rFVIIIFc
16 Recruiting Study of Recombinant Factor IX Product, IB1001, in Subjects With Hemophilia B
Condition: Hemophilia B
Interventions: Biological: IB1001 (On-Demand);   Biological: IB1001 (Prophylaxis)
17 Recruiting Joint Status in Subjects With Severe Hemophilia A in Relation to Different Treatment Regimens
Condition: Hemophilia A
Intervention: Procedure: No Drug
18 Recruiting Health Related Quality of Life of Youth and Young Adults With Hemophilia A
Condition: Hemophilia A
Intervention:
19 Recruiting Trial to Evaluate the Efficacy and Safety of a New Formulation of Kogenate for Hemophilia A
Conditions: Blood Coagulation Disorders;   Hemophilia A
Interventions: Biological: Recombinant Factor VIII (Kogenate PF, BAY81-8973);   Biological: Recombinant Factor VIII (Kogenate FS, BAY14-2222)
20 Recruiting Study of First TIME Immunotolerance Induction in Severe Hemophilia A Patients With Inhibitor at High Risk of Failure: Comparison With FVIII Concentrates With or Without Von Willebrand Factor - RES.I.S.T. Naive
Condition: Severe Hemophilia A
Interventions: Drug: FVIII;   Drug: FVIII/VWF concentrates

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