7 studies found for: Open Studies | "Tay-Sachs Disease"
Gene Therapy for Tay-Sachs Disease
|2||Not yet recruiting||
Synergistic Enteral Regimen for Treatment of the Gangliosidoses
A Natural History Study of Hexosaminidase Deficiency
HSCT for High Risk Inherited Inborn Errors
|5||Not yet recruiting||
Evaluating the Efficacy of a Web-based Educational Module Prior to Carrier Genetic Screening in Individuals of Ashkenazi Jewish Descent.
Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal Disorders
Fetal Umbilical Cord Blood (UCB) Transplant for Lysosomal Storage Diseases
† Indicates status has not been verified in more than two years