3 studies found for: Open Studies | "Tay-Sachs Disease"
A Natural History Study of Hexosaminidase Deficiency in Infantile Tay-Sachs Disease
Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal Disorders
Fetal Umbilical Cord Blood (UCB) Transplant for Lysosomal Storage Diseases
† Indicates status has not been verified in more than two years