18 studies found for:    Open Studies | "Muscular Atrophy, Spinal"
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Open Studies | "Muscular Atrophy, Spinal"
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Rank Status Study
1 Recruiting Clinical Assessment of Spinal Muscular Atrophy Type II and III (SMA Europe)
Condition: Spinal Muscular Atrophy
Intervention: Other: Functional tests
2 Recruiting Infants With Spinal Muscular Atrophy Type I
Condition: Spinal Muscular Atrophy
Intervention:
3 Recruiting International SMA Patient Registry
Condition: Muscular Atrophy, Spinal
Intervention:
4 Recruiting A Study to Assess the Safety and Pharmacokinetics of ISIS SMNRx in Infants With Spinal Muscular Atrophy
Condition: Spinal Muscular Atrophy
Intervention: Drug: ISIS-SMNRx
5 Recruiting An Open-label Safety, Tolerability and Dose-range Finding Study of Multiple Doses of ISIS SMNRx in Patient With Spinal Muscular Atrophy
Condition: Spinal Muscular Atrophy
Intervention: Drug: ISIS-SMNRx
6 Recruiting Clinical Trial of Exercise in Patients With Spinal Muscular Atrophy (SMA)
Conditions: Spinal Muscular Atrophy;   Neuromuscular Disease
Intervention: Other: Exercise
7 Recruiting An Open-label Safety and Tolerability Study of ISIS SMNRx in Patients With Spinal Muscular Atrophy Who Previously Participated in ISIS 396443-CS1
Condition: Spinal Muscular Atrophy
Intervention: Drug: ISIS-SMNRx
8 Recruiting Spinal Muscular Atrophy (SMA) Biomarkers Study in the Immediate Postnatal Period of Development
Condition: Spinal Muscular Atrophy (SMA)
Intervention:
9 Not yet recruiting Valproate and Levocarnitine in Children With Spinal Muscular Atrophy
Condition: Spinal Muscular Atrophy
Interventions: Drug: Valproate, Levocarnitine;   Drug: Placebo
10 Unknown  Motor Development and Orthoses in Spinal Muscular Atrophy (SMA)
Condition: Spinal Muscular Atrophy
Intervention:
11 Recruiting SMN Copy Number Distribution in Mali, West Africa
Condition: Spinal Muscular Atrophy
Intervention:
12 Unknown  Establishing Novel Detection Techniques for Various Genetic-Related Diseases by Applying DHPLC Platform.
Conditions: Spinal Muscular Atrophy;   Neonatal Hyperbilirubinemia;   Colon Cancer
Intervention:
13 Unknown  Quantitative Analysis of SMN1 and SMN2 Gene Based on DHPLC System
Condition: Spinal Muscular Atrophy
Intervention:
14 Recruiting Multi-disease Carrier Screening Test Validation
Conditions: Spinal Muscular Atrophy (SMA);   Carrier Screening;   Genetic Testing
Intervention: Procedure: Blood draw
15 Recruiting Flu Vaccine Study in Neuromuscular Patients 2011
Conditions: Duchenne Muscular Dystrophy;   Spinal Muscular Atrophy;   Congenital Muscular Dystrophy
Intervention: Biological: 2011-2012 seasonal flu vaccine
16 Recruiting Short and Long Term Treatment With 4-AP in Ambulatory SMA Patients
Condition: Spinal Muscular Atrophy
Interventions: Drug: 4-aminopyridine (dalfampridine, Ampyra);   Drug: Placebo
17 Recruiting Effect of Functional Exercise in Patients With Spinal Bulbar Muscular Atrophy
Condition: Motor Neuron Disease
Interventions: Behavioral: A functional exercise program;   Behavioral: A stretching exercise program
18 Unknown  Safety and Tolerability of Anakinra in Combination With Riluzol in Amyotrophic Lateral Sclerosis
Condition: Amyotrophic Lateral Sclerosis (ALS)
Intervention: Drug: Anakinra

Indicates status has not been verified in more than two years