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12 studies found for:    "spinal muscular atrophy with respiratory distress" OR "Infantile Spinal Muscular Atrophy" OR "Spinal Muscular Atrophies of Childhood"

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Rank Status Study
1 Terminated
Has Results 		Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type I
Condition: Spinal Muscular Atrophy Type I
Intervention: Drug: sodium phenylbutyrate
2 Completed CARNIVAL Type I: Valproic Acid and Carnitine in Infants With Spinal Muscular Atrophy (SMA) Type I
Condition: Spinal Muscular Atrophy Type I
Intervention: Drug: Valproic Acid and Levocarnitine
3 Recruiting Palliative Care in Spinal Muscular Atrophy (SMA) 1
Condition: Spinal Muscular Atrophy 1
Intervention: Other: Follow-up diary and questionnaire
4 Completed A Pilot Therapeutic Trial Using Hydroxyurea in Type I Spinal Muscular Atrophy Patients
Condition: Muscular Atrophy, Spinal
Intervention: Drug: Hydroxyurea
5 Recruiting Infants With Spinal Muscular Atrophy Type I
Condition: Spinal Muscular Atrophy
Intervention:
6 Active, not recruiting Safety and Efficacy of Olesoxime (TRO19622) in 3-25 Years SMA Patients.
Conditions: Spinal Muscular Atrophy Type II;   Spinal Muscular Atrophy Type III Non Ambulant
Interventions: Drug: Olesoxime;   Drug: Placebo
7 Unknown † A Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy Patients
Condition: Muscular Atrophy, Spinal
Intervention: Drug: Hydroxyurea
8 Recruiting Clinical Assessment of Spinal Muscular Atrophy Type II and III (SMA Europe)
Condition: Spinal Muscular Atrophy
Intervention: Other: Functional tests
9 Completed Pilot Study of Growth Hormon to Treat SMA Typ II and III
Condition: Muscular Atrophy, Spinal
Interventions: Drug: somatotropin;   Drug: Placebo
10 Terminated
Has Results 		Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Types II or III
Conditions: Spinal Muscular Atrophy Type II;   Spinal Muscular Atrophy Type III
Intervention: Drug: sodium phenylbutyrate
11 Recruiting International SMA Patient Registry
Condition: Muscular Atrophy, Spinal
Intervention:
12 Completed A Pilot Study of Biomarkers for Spinal Muscular Atrophy
Condition: Spinal Muscular Atrophy
Intervention:
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† Indicates status has not been verified in more than two years