96 studies found for:    "mucopolysaccharidosis type IV"
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Rank Status Study
21 Unknown  Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome)
Conditions: Mucopolysaccharidosis IVA;   Morquio A Syndrome;   MPS IVA
Intervention: Drug: BMN 110
22 Unknown  Safety and Exercise Study of BMN 110 for Morquio A Syndrome
Conditions: Mucopolysaccharidosis IVA;   Morquio A Syndrome;   MPS IVA
Intervention: Drug: BMN 110
23 Active, not recruiting Pamidronate to Treat Osteogenesis Imperfecta in Children
Condition: Osteogenesis Imperfecta
Intervention: Drug: Pamidronate (Aredia)
24 Completed Phase III Randomized Study of Interferon Gamma in Children With Severe, Congenital Osteopetrosis
Condition: Osteopetrosis
Interventions: Drug: calcitriol;   Drug: interferon gamma
25 Active, not recruiting Arimidex in McCune Albright Syndrome
Condition: McCune-Albright Syndrome
Intervention: Drug: Arimidex 1 mg
26 Recruiting MT2013-31:Allo BMT for Metabolic Disorders, Osteopetrosis and Males With Rett Syndrome
Conditions: Mucopolysaccharidosis I;   Mucopolysaccharidosis II;   Mucopolysaccharidosis VI;   Mucopolysaccharidosis VII;   Hurler Syndrome;   Hunter Syndrome;   Maroteaux Lamy Syndrome;   Sly Syndrome;   Glycoprotein Metabolic Disorders;   Alpha Mannosidosis;   Fucosidosis;   Aspartylglucosaminuria;   Adrenoleukodystrophy;   Peroxisomal Disorders;   Osteopetrosis;   Rett Syndrome;   Sphingolipidosis;   Gangliosidosis;   Globoid Cell Leukodystrophy;   Metachromatic Leukodystrophy;   Niemann Pick B;   Niemann Pick C Subtype 2;   I-cell Disease
Interventions: Procedure: blood stem cell transplant;   Drug: Rabbit Anti-Thymocyte Globulin (ATG);   Drug: Fludarabine;   Drug: Busulfan;   Drug: Cyclophosphamide;   Drug: Cyclosporine A (CSA);   Drug: Methylprednisolone;   Drug: Mycophenolate Mofetil (MMF);   Drug: Granulocyte-Colony Stimulating Factor (G-CSF);   Drug: Granulocyte-Macrophage Colony-Stimulating Factor (GM-CSF);   Drug: N-acetylcysteine;   Drug: Celecoxib;   Drug: Vitamin E;   Drug: Alpha Lipoic Acid
27 Active, not recruiting Growth Hormone Therapy in Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Intervention: Other: Growth hormone
28 Enrolling by invitation C-Type Natriuretic Peptide and Achondroplasia
Conditions: Achondroplasia;   Hypochondroplasia
Intervention:
29 Unknown  Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells
Conditions: Sickle Cell Disease;   Thalassemia;   Anemia;   Granuloma;   Wiskott-Aldrich Syndrome;   Chediak Higashi Syndrome;   Osteopetrosis;   Neutropenia;   Thrombocytopenia;   Hurler Disease;   Niemann-Pick Disease;   Fucosidosis
Intervention: Procedure: Hematopoietic stem cell transplantation
30 Active, not recruiting
Has Results
Faslodex in McCune Albright Syndrome
Conditions: Puberty, Precocious;   McCune-Albright Syndrome
Intervention: Drug: Fulvestrant
31 Completed Zoledronic Acid in Children (1 -17 Years) With Severe Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Intervention: Drug: Zoledronic Acid
32 Completed Marrow Mesenchymal Cell Therapy for Osteogenesis Imperfecta: A Pilot Study
Condition: Osteogenesis Imperfecta
Intervention: Procedure: Bone marrow transplant
33 Completed Bisphosphonate Therapy for Osteogenesis Imperfecta
Conditions: Osteogenesis Imperfecta;   Osteoporosis;   Paget Disease of Bone
Interventions: Drug: Alendronate;   Drug: Pamidronate
34 Completed Immune Response in the SAPHO Syndrome
Condition: SAPHO Syndrome
Intervention:
35 Terminated
Has Results
Reduced Intensity AlloTransplant For Osteopetrosis
Condition: Osteopetrosis
Interventions: Procedure: Stem Cell or Umbilical Cord Blood Transplantation;   Drug: Campath, Busulfan, Clofarabine;   Procedure: Total Lymphoid Irradiation
36 Completed Treatment of Severe Osteogenesis Imperfecta by Allogeneic Bone Marrow Transplantation
Condition: Osteogenesis Imperfecta
Interventions: Other: Bone Marrow Cell Transplantation;   Radiation: Irradiation, Total Body;   Drug: Cyclophosphamide;   Drug: Cyclosporin;   Procedure: Mesenchymal Stem Cell Transplantation;   Drug: Busulfan
37 Terminated A Single Centre Study to Assess the Long-term Performance of the Pinnacle™ Cup With a Ceramic-on-ceramic Bearing in Primary Total Hip Replacement
Conditions: Rheumatoid Arthritis;   Osteoarthritis;   Post-traumatic Arthritis;   Collagen Disorders;   Avascular Necrosis;   Traumatic Femoral Fractures;   Nonunion of Femoral Fractures;   Congenital Hip Dysplasia;   Slipped Capital Femoral Epiphysis
Intervention: Device: Pinnacle™ Acetabular System
38 Active, not recruiting An Efficacy and Safety Trial of Intravenous Zoledronic Acid in Infants Less Than One Year of Age, With Severe Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Intervention: Drug: Zoledronic Acid
39 Unknown  Antioxidant Supplementation in Patients With Kashin-Beck Disease
Condition: Kashin-Beck Disease
Intervention: Dietary Supplement: Biological Antioxidant Supplementation
40 Recruiting Screening and Natural History of Patients With Polyostotic Fibrous Dysplasia and McCune-Albright Syndrome
Condition: Polyostotic Fibrous Dysplasia
Intervention:

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Indicates status has not been verified in more than two years