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96 studies found for:    "mucopolysaccharidosis type IV"
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Rank Status Study
21 Active, not recruiting BMN 110 Phase 3B in Australian Patients
Condition: Mucopolysaccharidosis IVA (Morquio A Syndrome)
Intervention: Drug: BMN 110
22 Active, not recruiting Efficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation
Conditions: Mucopolysaccharidosis IVA;   Morquio A Syndrome;   MPS IVA
Intervention: Drug: BMN 110
23 Active, not recruiting Rubinstein-Taybi Syndrome: Functional Imaging and Therapeutic Trial
Condition: Rubinstein-Taybi Syndrome
Interventions: Drug: sodium valproate;   Drug: Placebo
24 Unknown  Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells
Conditions: Sickle Cell Disease;   Thalassemia;   Anemia;   Granuloma;   Wiskott-Aldrich Syndrome;   Chediak Higashi Syndrome;   Osteopetrosis;   Neutropenia;   Thrombocytopenia;   Hurler Disease;   Niemann-Pick Disease;   Fucosidosis
Intervention: Procedure: Hematopoietic stem cell transplantation
25 Completed Effects of Letrozole on Precocious Puberty Due to McCune Albright Syndrome
Conditions: McCune Albright Syndrome;   Polyostotic Fibrous Dysplasia;   Precocious Puberty
Intervention: Drug: Letrozole
26 Active, not recruiting Pamidronate to Treat Osteogenesis Imperfecta in Children
Condition: Osteogenesis Imperfecta
Intervention: Drug: Pamidronate (Aredia)
27 Completed Clinical Assessment of Patients With High Bone Mass Due to Mutation in Lrp5
Condition: Osteopetrosis
Intervention:
28 Recruiting Evaluation and Intervention for the Effects of Osteogenesis Imperfecta
Conditions: Dwarfism;   Osteogenesis Imperfecta
Intervention:
29 Terminated A Single Centre Study to Assess the Long-term Performance of the DePuy ASR™ System in Primary Hip Resurfacing Surgery
Conditions: Rheumatoid Arthritis;   Osteoarthritis;   Post-traumatic Arthritis;   Collagen Disorders;   Avascular Necrosis;   Nonunion of Femoral Fractures;   Congenital Hip Dysplasia;   Slipped Capital Femoral Epiphysis.
Intervention: Device: DePuy ASR™ Hip System
30 Recruiting The Effect of Treatment With Teriparatide and Zoledronic Acid in Patients With Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Interventions: Drug: Zoledronic acid;   Drug: Teriparatide;   Drug: placebo zoledronic acid;   Drug: placebo teriparatide
31 Terminated A Single Centre Study to Assess the Long-term Performance of the Pinnacle™ Cup With a Ceramic-on-ceramic Bearing in Primary Total Hip Replacement
Conditions: Rheumatoid Arthritis;   Osteoarthritis;   Post-traumatic Arthritis;   Collagen Disorders;   Avascular Necrosis;   Traumatic Femoral Fractures;   Nonunion of Femoral Fractures;   Congenital Hip Dysplasia;   Slipped Capital Femoral Epiphysis
Intervention: Device: Pinnacle™ Acetabular System
32 Terminated rhPTH Therapy for Low Turnover Bone Fragility
Condition: Osteopetrosis
Intervention: Drug: rhPTH
33 Completed A Study of the Effects of Pegvisomant on Growth Hormone Excess in McCune-Albright Syndrome
Conditions: McCune Albright Syndrome;   Polyostotic Fibrous Dysplasia
Intervention: Drug: Pegvisomant
34 Recruiting Screening and Natural History of Patients With Polyostotic Fibrous Dysplasia and McCune-Albright Syndrome
Condition: Polyostotic Fibrous Dysplasia
Intervention:
35 Unknown  A Randomised Single Centre Study to Compare the Long-Term Wear Characteristics of Marathon™ and Enduron™ Polyethylene Cup Liners in Primary Total Hip Replacement
Conditions: Osteoarthritis;   Post-Traumatic Arthritis;   Collagen Disorders;   Avascular Necrosis;   Traumatic Femoral Fractures;   Nonunion of Femoral Fractures;   Congenital Hip Dysplasia;   Slipped Capital Femoral Epiphysis
Interventions: Device: Marathon™;   Device: Enduron
36 Recruiting TOCILIZUMAB IN FIBROUS DYSPLASIA OF BONE
Condition: Fibrous Dysplasia of Bone
Interventions: Drug: Tocilizumab;   Drug: Placebo
37 Terminated A Multi-centre Study to Assess the Long-term Performance of the Summit™ Hip in Primary Total Hip Replacement
Conditions: Rheumatoid Arthritis;   Osteoarthritis;   Post-traumatic Arthritis;   Collagen Disorders;   Avascular Necrosis;   Traumatic Femoral Fractures;   Nonunion of Femoral Fractures;   Congenital Hip Dysplasia;   Slipped Capital Femoral Epiphysis
Intervention: Device: Summit Tapered Hip System
38 Not yet recruiting Growth Hormone for Osteoporosis Pseudoglioma Syndrome
Condition: Osteoporosis Pseudoglioma Syndrome
Intervention: Biological: Human recombinant growth hormone
39 Terminated A Multi-centre Study to Assess the Long-term Performance of the DePuy ASR™ System in Primary Hip Resurfacing Surgery
Conditions: Rheumatoid Arthritis;   Osteoarthritis;   Post-traumatic Arthritis;   Collagen Disorders;   Avascular Necrosis;   Nonunion of Femoral Fractures;   Congenital Hip Dysplasia;   Slipped Capital Femoral Epiphysis.
Intervention: Device: DePuy ASR Hip System
40 Terminated Establishing the Genetic Profile of Multiple Hereditary Exostoses (HME) in Families of BC
Condition: Exostoses, Multiple Hereditary
Intervention:

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Indicates status has not been verified in more than two years