83 studies found for:    "mucopolysaccharidosis type IV"
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Rank Status Study
21 Active, not recruiting Safety and Exercise Study of BMN 110 for Morquio A Syndrome
Conditions: Mucopolysaccharidosis IVA;   Morquio A Syndrome;   MPS IVA
Intervention: Drug: BMN 110
22 Active, not recruiting Pamidronate to Treat Osteogenesis Imperfecta in Children
Condition: Osteogenesis Imperfecta
Intervention: Drug: Pamidronate (Aredia)
23 Completed Phase III Randomized Study of Interferon Gamma in Children With Severe, Congenital Osteopetrosis
Condition: Osteopetrosis
Interventions: Drug: calcitriol;   Drug: interferon gamma
24 Active, not recruiting Arimidex in McCune Albright Syndrome
Condition: McCune-Albright Syndrome
Intervention: Drug: Arimidex 1 mg
25 Recruiting MT2013-31:Allo BMT for Metabolic Disorders, Osteopetrosis and Males With Rett Syndrome
Conditions: Mucopolysaccharidosis I;   Mucopolysaccharidosis II;   Mucopolysaccharidosis VI;   Mucopolysaccharidosis VII;   Hurler Syndrome;   Hunter Syndrome;   Maroteaux Lamy Syndrome;   Sly Syndrome;   Glycoprotein Metabolic Disorders;   Alpha Mannosidosis;   Fucosidosis;   Aspartylglucosaminuria;   Adrenoleukodystrophy;   Peroxisomal Disorders;   Osteopetrosis;   Rett Syndrome;   Sphingolipidosis;   Gangliosidosis;   Globoid Cell Leukodystrophy;   Metachromatic Leukodystrophy;   Niemann Pick B;   Niemann Pick C Subtype 2;   I-cell Disease
Interventions: Procedure: blood stem cell transplant;   Drug: Rabbit Anti-Thymocyte Globulin (ATG);   Drug: Fludarabine;   Drug: Busulfan;   Drug: Cyclophosphamide;   Drug: Cyclosporine A (CSA);   Drug: Methylprednisolone;   Drug: Mycophenolate Mofetil (MMF);   Drug: Granulocyte-Colony Stimulating Factor (G-CSF);   Drug: Granulocyte-Macrophage Colony-Stimulating Factor (GM-CSF);   Drug: N-acetylcysteine;   Drug: Celecoxib;   Drug: Vitamin E;   Drug: Alpha Lipoic Acid
26 Active, not recruiting Growth Hormone Therapy in Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Intervention: Other: Growth hormone
27 Enrolling by invitation C-Type Natriuretic Peptide and Achondroplasia
Conditions: Achondroplasia;   Hypochondroplasia
Intervention:
28 Unknown  Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells
Conditions: Sickle Cell Disease;   Thalassemia;   Anemia;   Granuloma;   Wiskott-Aldrich Syndrome;   Chediak Higashi Syndrome;   Osteopetrosis;   Neutropenia;   Thrombocytopenia;   Hurler Disease;   Niemann-Pick Disease;   Fucosidosis
Intervention: Procedure: Hematopoietic stem cell transplantation
29 Active, not recruiting
Has Results
Faslodex in McCune Albright Syndrome
Conditions: Puberty, Precocious;   McCune-Albright Syndrome
Intervention: Drug: Fulvestrant
30 Completed Zoledronic Acid in Children (1 -17 Years) With Severe Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Intervention: Drug: Zoledronic Acid
31 Completed Marrow Mesenchymal Cell Therapy for Osteogenesis Imperfecta: A Pilot Study
Condition: Osteogenesis Imperfecta
Intervention: Procedure: Bone marrow transplant
32 Completed Bisphosphonate Therapy for Osteogenesis Imperfecta
Conditions: Osteogenesis Imperfecta;   Osteoporosis;   Paget Disease of Bone
Interventions: Drug: Alendronate;   Drug: Pamidronate
33 Completed Immune Response in the SAPHO Syndrome
Condition: SAPHO Syndrome
Intervention:
34 Terminated
Has Results
Reduced Intensity AlloTransplant For Osteopetrosis
Condition: Osteopetrosis
Interventions: Procedure: Stem Cell or Umbilical Cord Blood Transplantation;   Drug: Campath, Busulfan, Clofarabine;   Procedure: Total Lymphoid Irradiation
35 Completed Treatment of Severe Osteogenesis Imperfecta by Allogeneic Bone Marrow Transplantation
Condition: Osteogenesis Imperfecta
Interventions: Other: Bone Marrow Cell Transplantation;   Radiation: Irradiation, Total Body;   Drug: Cyclophosphamide;   Drug: Cyclosporin;   Procedure: Mesenchymal Stem Cell Transplantation;   Drug: Busulfan
36 Active, not recruiting An Efficacy and Safety Trial of Intravenous Zoledronic Acid in Infants Less Than One Year of Age, With Severe Osteogenesis Imperfecta
Condition: Osteogenesis Imperfecta
Intervention: Drug: Zoledronic Acid
37 Unknown  Antioxidant Supplementation in Patients With Kashin-Beck Disease
Condition: Kashin-Beck Disease
Intervention: Dietary Supplement: Biological Antioxidant Supplementation
38 Recruiting Screening and Natural History of Patients With Polyostotic Fibrous Dysplasia and McCune-Albright Syndrome
Condition: Polyostotic Fibrous Dysplasia
Intervention:
39 Completed A Study of the Effects of Pegvisomant on Growth Hormone Excess in McCune-Albright Syndrome
Conditions: McCune Albright Syndrome;   Polyostotic Fibrous Dysplasia
Intervention: Drug: Pegvisomant
40 Completed Alendronate to Treat Polyostotic Fibrous Dysplasia and McCune-Albright Syndrome
Condition: Polyostotic Fibrous Dysplasia
Intervention: Drug: Fosamax (Alendronate)

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Indicates status has not been verified in more than two years