6 studies found for: "mucolipidosis type II" OR "Mucolipidosis Type II"
Stem Cell Transplantation for Hurler
Longitudinal Studies of the Glycoproteinoses
Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation
HSCT for High Risk Inherited Inborn Errors
Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal Disorders
ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases
† Indicates status has not been verified in more than two years