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91 studies found for:    "inclusion body myopathy with early-onset Paget disease and frontotemporal dementia" OR "Frontotemporal Dementia" OR "Paget's Disease of Bone"
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Rank Status Study
21 Completed A Research Study to Test the Effectiveness of MK0217 in Patients With Paget's Bone Disease (0217-206)(COMPLETED)
Condition: Paget's Disease of Bone
Intervention: Drug: alendronate
22 Recruiting Phase 1/2 Study of Vorinostat Therapy in Niemann-Pick Disease, Type C1
Condition: Neimann-Pick Disease
Intervention: Drug: Vorinostat
23 Completed Longitudinal Study of Cognition With Niemann-Pick Disease, Type C
Condition: Niemann-Pick Disease, Type C
Intervention:
24 Completed
Has Results
Biomarker Validation for Niemann-Pick Disease, Type C: Safety and Efficacy of N-Acetyl Cysteine
Condition: Niemann-Pick Disease, Type C
Intervention: Drug: N-Acetyl Cysteine
25 Completed
Has Results
Safety and Efficacy Trial With Zoledronic Acid for the Treatment of Paget's Disease of Bone, Including an Extended Observation Period
Condition: Paget's Disease of Bone
Interventions: Drug: Zoledronic Acid;   Drug: Risedronate;   Drug: Placebo to Risedronate;   Drug: Placebo to Zoledronic Acid;   Dietary Supplement: Calcium and Vitamin D
26 Recruiting Evaluation of Biochemical Markers and Clinical Investigation of Niemann-Pick Disease, Type C
Condition: Neimann-Pick Disease, Type C
Intervention:
27 Completed Performance of AclarusDx™, a Blood-Based Transcriptomic Test for AD, in US Patients Newly Referred to a Memory Center
Conditions: Alzheimer's Disease;   Mild Cognitive Impairment;   Vascular Dementia;   Fronto-temporal Dementia;   Primary Progressive Aphasia;   Parkinson' Disease Dementia;   Mixed Dementia
Intervention:
28 Terminated Safety Study of rhASM Enzyme Replacement Therapy in Adults With Acid Sphingomyelinase Deficiency (Niemann-Pick Disease)
Conditions: Acid Sphingomyelinase Deficiency;   Niemann-Pick Disease
Intervention: Drug: rhASM
29 Recruiting Hydroxypropyl Beta Cyclodextrin for Niemann-Pick Type C1 Disease
Condition: Niemann-Pick Disease, Type C1
Intervention: Drug: 2-hydroxypropyl-beta-cyclodextrin
30 Unknown  Language Treatment for Progressive Aphasia
Conditions: Primary Progressive Aphasia;   Nonfluent Progressive Aphasia;   Semantic Dementia
Intervention: Behavioral: Errorless learning
31 Recruiting Sodium Risedronate Tablets - Special Drug Use Surveillance in Patients With Osseous Paget's Disease (All-case Surveillance) -48-week Surveillance −
Condition: Osseous Paget's Disease
Intervention: Drug: Sodium risedronate
32 Recruiting Genetics of Familial and Sporadic ALS
Conditions: Amyotrophic Lateral Sclerosis;   Familial Amyotrophic Lateral Sclerosis;   Amyotrophic Lateral Sclerosis and Frontotemporal Dementia;   Lou Gehrig's Disease;   Motor Neuron Disease;   Primary Lateral Sclerosis
Intervention: Other: Genetic study of ALS families
33 Recruiting Young Onset Dementia - the Difficult Diagnosis and the Stressful Life for the Whole Family
Conditions: Frontotemporal Dementia;   Alzheimer's Disease.
Intervention:
34 Active, not recruiting Computational Tools for Early Diagnosis of Memory Disorders
Conditions: Alzheimer Disease;   Frontotemporal Dementia;   Dementia, Vascular;   Mild Cognitive Impairment
Intervention:
35 Enrolling by invitation A Composite MR Neuroimaging Marker for Alzheimer's Disease
Conditions: Alzheimer's Disease;   Mild Cognitive Impairment;   Frontotemporal Dementia
Intervention:
36 Active, not recruiting Davunetide (AL-108) in Predicted Tauopathies - Pilot Study
Conditions: Predicted Tauopathies, Including:;   Progressive Supranuclear Palsy;   Frontotemporal Dementia With Parkinsonism Linked to Chromosome 17;   Corticobasal Degeneration Syndrome;   Progressive Nonfluent Aphasia
Interventions: Drug: davunetide (AL-108, NAP);   Drug: Placebo nasal spray
37 Recruiting Biomarker for Niemann Pick Type C Disease
Conditions: Niemann-Pick Disease;   Niemann-Pick Disease, Type C
Intervention:
38 Terminated
Has Results
Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism
Conditions: Hurler's Syndrome;   Maroteaux-Lamy Syndrome;   Sly Syndrome;   Alpha Mannosidosis;   Fucosidosis;   Aspartylglucosaminuria;   Sphingolipidoses;   Krabbe Disease;   Wolman's Disease;   Niemann-Pick Disease Type B;   Niemann-Pick Disease, Type C
Interventions: Procedure: Stem Cell Transplantation;   Drug: Cyclophosphamide;   Drug: Campath-1H;   Drug: Busulfan
39 Completed Treatment Study of Frontotemporal Dementia
Condition: Frontotemporal Lobar Degeneration
Intervention:
40 Terminated Amantadine for the Treatment of Behavioral Disturbance in Frontotemporal Dementia (FTD)
Condition: Dementia
Intervention: Drug: amantadine

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Indicates status has not been verified in more than two years