Lithium and Acetate for Canavan Disease
GTA-Glyceryltriacetate for Canavan Disease
Oral Glyceryl Triacetate (GTA) in Newborns With Canavan
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Evaluating the Efficacy of a Web-based Educational Module Prior to Carrier Genetic Screening in Individuals of Ashkenazi Jewish Descent.
ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases
† Indicates status has not been verified in more than two years