93 studies found for:    "Muscular Dystrophy, Duchenne"
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Study Details
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Rank Status Study
1 Completed Phase 2b Study of PTC124 in Duchenne/Becker Muscular Dystrophy (DMD/BMD)
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention: Drug: PTC124
2 Suspended Revatio for Heart Disease in Duchenne Muscular Dystrophy and Becker Muscular Dystrophy
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention: Drug: Sildenafil
3 Completed CRD007 for the Treatment of Duchenne Muscular Dystrophy, Becker Muscular Dystrophy and Symptomatic Carriers
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention: Drug: CRD007
4 Terminated Phase 2b Extension Study of Ataluren (PTC124) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention: Drug: Ataluren (PTC124)
5 Suspended Study of Ataluren (PTC124®) in Nonambulatory Patients With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD)
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention: Drug: Ataluren (PTC124)
6 Recruiting Double Push Acoustic Radiation Force (DP ARF) Ultrasound for Monitoring Degeneration in Duchenne Muscular Dystrophy
Condition: Muscular Dystrophy, Duchenne
Intervention:
7 Active, not recruiting Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD)
Conditions: Muscular Dystrophy, Duchenne;   Ambulatory Care
Intervention: Drug: Idebenone (CATENA®)
8 Unknown  Ramipril Versus Carvedilol in Duchenne and Becker Patients
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Interventions: Drug: carvedilol;   Drug: ramipril
9 Enrolling by invitation Effect of EPA and DHA in the Inflammation and Metabolic Disorders in DMD/DMB Patients
Condition: Muscular Dystrophy, Duchenne
Interventions: Dietary Supplement: EPA and DHA;   Dietary Supplement: Placebo Comparator: Sunflower oil
10 Completed Pentoxifylline in Duchenne Muscular Dystrophy
Condition: Muscular Dystrophy, Duchenne
Intervention: Drug: Pentoxifylline
11 Completed Effect of Oral Glutamine on Muscle Mass and Function in Duchenne Muscular Dystrophy
Condition: Muscular Dystrophy, Duchenne
Interventions: Drug: L-Glutamine;   Drug: placebo
12 Completed Creatine and Glutamine in Steroid-Naive Duchenne Muscular Dystrophy
Condition: Muscular Dystrophy, Duchenne
Interventions: Drug: Creatine Monohydrate;   Drug: Glutamine
13 Completed A Multicenter Randomized Placebo-Controlled Double-Blind Study to Assess Efficacy and Safety of Glutamine and Creatine Monohydrate in Duchenne Muscular Dystrophy (DMD)
Condition: Muscular Dystrophy, Duchenne
Interventions: Drug: glutamine;   Drug: creatine monohydrate
14 Recruiting Phase 3 Study of Ataluren in Patients With Nonsense Mutation Duchenne Muscular Dystrophy
Conditions: Muscular Dystrophy, Duchenne;   Muscular Dystrophies;   Muscular Disorders, Atrophic;   Muscular Diseases;   Musculoskeletal Diseases;   Neuromuscular Diseases;   Nervous System Diseases;   Genetic Diseases, X-Linked;   Genetic Diseases, Inborn
Interventions: Drug: Ataluren;   Drug: Placebo
15 Completed High-dose Prednisone in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Drug: Prednisone
16 Recruiting Study of Ataluren for Previously Treated Patients With nmDBMD in Europe, Israel, Australia, and Canada
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy;   Dystrophinopathy
Intervention: Drug: Ataluren
17 Recruiting Study of Ataluren for Previously Treated Patients With nmDBMD in the US
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention: Drug: Ataluren
18 Completed Gentamicin Treatment of Muscular Dystrophy
Conditions: Becker Muscular Dystrophy;   Duchenne Muscular Dystrophy
Intervention: Drug: Gentamicin
19 Recruiting Early Treatment of Cardiomyopathy in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Interventions: Drug: eplerenone;   Drug: placebo
20 Unknown  Safety Study of Flavocoxid in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Drug: Flavocoxid

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Indicates status has not been verified in more than two years