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Found 57 studies with search of: "Muscular Dystrophies"
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1 Recruiting Evaluation of Limb-Girdle Muscular Dystrophy
Conditions: Becker Muscular Dystrophy;   Limb-Girdle Muscular Dystrophy, Type 2A;   Calpain-3 Deficiency;   Limb-Girdle Muscular Dystrophy, Type 2B;   Miyoshi Myopathy;   Dysferlin Deficiency;   Limb-Girdle Muscular Dystrophy, Type 2I;   FKRP-deficiency
Intervention:
2 Recruiting Safety Study of Transvenous Limb Perfusion in Human Muscular Dystrophy
Conditions: Muscular Dystrophies;   Becker Muscular Dystrophy;   Limb-Girdle Muscular Dystrophy
Intervention: Other: Retrograde high pressure transvenous perfusion with normal saline
3 Active, not recruiting Phase 2b Study of PTC124 in Duchenne/Becker Muscular Dystrophy (DMD/BMD)
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention: Drug: PTC124
4 Completed Gentamicin Treatment of Muscular Dystrophy
Conditions: Becker Muscular Dystrophy;   Duchenne Muscular Dystrophy
Intervention: Drug: Gentamicin
5 Completed Study Evaluating MYO-029 in Adult Muscular Dystrophy
Conditions: Becker Muscular Dystrophy;   Facioscapulohumeral Muscular Dystrophy;   Limb-Girdle Muscular Dystrophy
Intervention: Drug: MYO-029
6 Recruiting Phase 2b Extension Study of Ataluren (PTC124) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention: Drug: Ataluren (PTC124)
7 Not yet recruiting Study of Ataluren (PTC124®) in Nonambulatory Patients With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD)
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Intervention: Drug: Ataluren (PTC124)
8 Recruiting Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
Conditions: Myotonic Dystrophy;   Muscular Dystrophy, Facioscapulohumeral;   Muscular Dystrophy
Intervention:
9 Recruiting Molecular Analysis of Patients With Neuromuscular Disease
Conditions: Limb-Girdle Muscular Dystrophy;   Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy;   Facioscapulohumeral Muscular Dystrophy
Intervention:
10 Recruiting Ramipril Versus Carvedilol in Duchenne and Becker Patients
Conditions: Duchenne Muscular Dystrophy;   Becker Muscular Dystrophy
Interventions: Drug: carvedilol;   Drug: ramipril
11 Recruiting Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)
Condition: Muscular Dystrophies
Interventions: Genetic: rAAV1.tMCK.human-alpha-sarcoglycan- First cohort;   Genetic: Genetic: rAAV1.tMCK.human-alpha-sarcoglycan- Second cohort
12 Active, not recruiting The Efficacy of Using Far Infrared Radiation to Manage Muscular Dystrophies
Condition: Muscular Dystrophies
Intervention: Radiation: Far Infrared Radiation
13 Completed High-Dose Prednisone in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Drug: Prednisone
14 Active, not recruiting Safety Study of Mini-Dystrophin Gene to Treat Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Gene Transfer: rAAV vector expressing Mini-Dystrophin with CMV promoter
15 Recruiting The Preventive Efficacy of Carvedilol on Cardiac Dysfunction in Duchenne Muscular Dystrophy
Conditions: Duchenne Muscular Dystrophy;   Cardiomyopathies
Intervention: Drug: Carvedilol
16 Completed Safety and Efficacy Study of PTC124 in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Drug: PTC124
17 Recruiting A Clinical Evaluation of FKRP Muscular Dystrophy
Condition: Muscular Dystrophy
Intervention:
18 Recruiting Test-Retest Reliability of Pulmonary Function Tests in Patients With Duchenne's Muscular Dystrophy
Conditions: Duchenne's Muscular Dystrophy;   Scoliosis
Intervention:
19 Active, not recruiting Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular Dystrophy
Condition: Duchenne Muscular Dystrophy
Intervention: Drug: AVI-4658 (PMO)
20 Active, not recruiting Phase 2a Extension Study of Ataluren (PTC124) in Duchenne Muscular Dystrophy (DMD)
Condition: Duchenne Muscular Dystrophy
Intervention: Drug: Ataluren

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